Efficacy and Safety Study of CC-5013 Monotherapy in Subjects With Myelodysplastic Syndromes
Myelodysplastic Syndromes
About this trial
This is an interventional treatment trial for Myelodysplastic Syndromes focused on measuring MDS, CC-5013, Revlimid, Celgene
Eligibility Criteria
Inclusion Criteria: Must understand and voluntarily sign an informed consent form. Age ≥ 18 years at the time of signing the informed consent form. Must be able to adhere to the study visit schedule and other protocol requirements. Diagnosis of low - or intermediate-1-risk IPSS (Appendix III) MDS without an abnormality of chromosome 5 involving a deletion between bands q31 and q33. Red blood cell (RBC) transfusion-dependent anemia defined as having received ≥ to 2 units of RBCs within 8 weeks of the first day of study drug treatment. Eastern Cooperative Oncology Group (ECOG) (Appendix IV) performance status score of 0, 1, or 2. Women of childbearing potential (WCBP) must have a negative serum or urine pregnancy test within 7 days of starting study drug. Sexually active WCBP must agree to use adequate contraceptive methods (oral, injectable, or implantable hormonal contraceptive; tubal ligation; intra-uterine device; barrier contraceptive with spermicide; or vasectomized partner) while on study drug. WCBP must agree to have pregnancy tests every 4 weeks while on study drug. Exclusion Criteria: Pregnant or lactating females. Prior therapy with lenalidomide. An abnormality of chromosome 5 involving a deletion between bands q31 and q33. Lab Abnormality: Absolute neutrophil count (ANC) <500 cells/mm3 (0.5 x 109/L) Lab Abnormality: Platelet count <50,000/mm3 (50 x 109/L) Lab Abnormality: Serum creatinine >2.5 mg/dL (221 mmol/L) Lab Abnormality: Serum glutamic oxaloacetic transaminase/Aspartate transaminase (SGOT/AST) or Serum glutamic pyruvic transaminase/Alanine transaminase (SGPT/ALT) >3.0 x upper limit of normal (ULN) Lab Abnormality: Serum total bilirubin >2.0 mg/dL (34 mmol/L) Prior ≥ grade 3 National Cancer Institute (NCI) Common Toxicity Criteria (CTC) (Appendix VI) allergic reaction/hypersensitivity to thalidomide. Prior ≥ grade 3 NCI CTC (Appendix VI) rash or any desquamation (blistering) while taking thalidomide. Clinically significant anemia due to factors such as iron, B12 or folate deficiencies, autoimmune or hereditary hemolysis or gastrointestinal bleeding If a marrow aspirate is not evaluable for storage iron, transferrin saturation must be > 20 % and serum ferritin not less than 50 ng/mL. Use of hematopoietic growth factors within 7 days of the first day of study drug treatment. Chronic use (>2 weeks) of greater than physiologic doses of a corticosteroid agent (dose equivalent to >10 mg/day of prednisone) within 28 days of the first day of study drug treatment. Use of experimental or standard drugs (i.e. chemotherapeutic, immunosuppressive, and cytoprotective agents) for the treatment of MDS within 28 days of the first day of study drug treatment. Prior history of malignancy other than MDS (except basal cell or squamous cell carcinoma or carcinoma in situ of the cervix or breast) unless the subject has been free of disease for greater than or equal to 3 years. Use of any other experimental therapy within 28 days of the first day of study drug treatment.
Sites / Locations
- Arizona Cancer Center
- Mayo Clinic
- Arizona Cancer Center
- Alta Bates Cancer Center
- Desert Hematology Oncology Medical Group, Inc.
- Stanford University Medical Center
- Florida Cancer Specialists
- Mayo Clinic
- Cancer & Blood Disease Center
- University of Miami- Sylvester Comp Cancer Center
- H. Lee Moffitt Cancer Center and Research Institute
- Northwest Georgia Oncology - Wellstar Cancer Research
- Rush Presbyterian-St. Luke's Medical Center
- University of Chicago Medical Center
- Midwest Cancer Research Group
- Indiana University Medical Center
- Johns Hopkins Oncology Center
- Dana-Farber Cancer Institute
- Wayne State University School of Medicine
- St. Luke's Oncology and Hematology Associates
- Mayo Clinic
- University of Nebraska Medical Center
- Roswell Park Cancer Institute
- Winthrop University Hospital
- St. Vincents Comprehensive Cancer Center
- New York Hospital- Cornell
- Memorial Sloan-Kettering Cancer Center
- Mt. Sinai Medical Center
- University of Rochester-James P. Wilmot Cancer Center
- Wake Forest University School of Medicine
- The Cleveland Clinic Foundation
- Oregon Health & Science University
- Kaiser Permanente Northwest Region
- Drexel University College of Medicine
- Western Pennsylvania Cancer Institute
- MD Anderson Cancer Center
- Swedish Cancer Institute
- Fred Hutchinson Cancer Research Center
- Royal Adelaide Hospital - SA Pathology Haematology
- Princess Alexandra Hospital - Haematology
- Royal Prince Alfred Hospital - Institute of Haematology
- Peter McCallum Cancer Institute - Directorate of Cancer Medecine
- Frankston Hospital-peninsula Health - Oncology Day Unit
- The Alfred Hospital - malignant haematology & stem cell transplantation
- Calvary Mater Newcastle - Haematology
- Border Medical Oncology
- Wollongong Hospital - Haematology
- UZ Gent - Hematology
- University Hospital Leuven - Hematology
- Cliniques Universitaires ULC de Mont-Godinne - Hematology
- Fakultní nemocnice Hradec Králové - Hematology
- Charles university Hospital - Internal Medicine
- Aalborg Sygemus - Haematology
- Aarhus University Hospital
- Odense University Hospital
- Vejle Hospital - Hematology
- CHU Angers - Service des maladies du sang
- Centre Hospitalier de la côte basque - Hematologie
- Centre Hospitalier Départemental Vendée - Onco-hematologie
- CHRU de Lille - Service des maladies du sang
- Institut Paoli Calmette - Hematology 1
- CHU Hôtel-Dieu - Hematologie
- Hôpital Saint Louis - Immuno-hematologie
- CHU Saint Antoine - Service des maladies du sang
- CHRU - Hôpital du Haut Lévêque - Centre François Magendie
- Centre Hospitalier Lyon sud - Hematologie
- CHRU Hôpital Purpan - Hematologie
- Hôpital Bretonneau - Hématologie & Thérapie cellulaire
- CHU Nancy - Hematologie
- Universitätsklinikum Essen, Klinik für Hämatologie
- Universitätsklinikum Heidelberg - Medizinische Klinik und Poliklinik V
- Universitätsklinikum Jena - Klinik fur Innere Medizin II-Hamatologie/Onkologie
- Universitätsklinikum Leipzig - Medizinische Klinik und Poliklinik II
- Universitätsklinikum Münster - Medizinische Klinik und Poliklinik A
- Universitätsklinikum Tübingen - Medizinische Klinik und Poliklinik - Abteilung II
- Universitätsklinikum Ulm - Klinik fur Innere Medizin III
- Universitätsklinikum Würzburg - Medizinische Klinik und Poliklinik II
- University of Athens - Alexandra Hospital; Clinical Therapeutics
- Università degli Studi di Bologna - Policlinico S. Orsola - Hematology
- AO Universitaria San Martino - hematooncology
- Fondazione "G. Pascale" - Hematology
- Ospedale San Luigi AO Luigi Gonzaga - Hematology
- Universita degli Studi di Padova - Clinical & Experimental Medicine
- Ospedale Guglielmo da Saliceto - hematooncology
- Unità di Ematologia Arcispedale S. Maria Nuova - Haematology
- Policlinico Umberto I, Università "La Sapienza" di Roma - Hematology
- A.O.U. San Giovanni Battista - Hematology
- VUMC - Hematology
- Erasmus Medical Center - Hematology
- University Medical Center - Hematology
- Medical Sciences - Hematology & BMT
- Moscow State Medical Institution Municipal Clinical Hospital n.a. S.P. Botkin - Hematology
- Russian Research Institute of Hematology and Blood Transfusion - Hematology
- State Higher Educational Institution St. Petersburg State Medical University - Onco-hematology
- Hospital Germans Trias i Pujol - Hematology
- Hospital Clinic i Provincial de Barcelona - Hematology
- Hospital de Donostia - Hematology
- Hospital de La Princesa - Hematology
- Hospital 12 de Octubre - Hematology
- Hospital de Salamanca - Hematology
- Hospital Universitario Marqués de Valdecilla - Hematology
- Hospital La Fe - Hematology
- Sahlgrenska Hospital, University of Goteborg - Hematology
- Karolinska University Hospital Huddinge - Center of hematology
- Karolinska University Hospital Solna- medicine
- Overlakare Medocomcentrum - Hematology
- Inselspital, Institut für Medizinische Onkologie
- Hôpitaux Universitaire de Genève - Oncologie
- Klinik und Poliklinik für Onkologie - UniversitätsSpital Zürich
- Royal Bournemouth Hospital - Haematology
- St James's University Hospital - Haematology
- St Bartholomew's Hospital - Medical Oncology
- King's College Hospital - Haematology Clinical Trials
- Freeman Hospital - Northern Centre for Cancer Care
- Nottingham City Hospital - Centre for Clinical Haematology
- Derriford Hospital - Haematology
- Royal hallamshire Hospital - Haematology
- Royal Marsden NHS Foundation Trust - Haematology
- Royal Wolverhampton hospitals trust - Research and development
Arms of the Study
Arm 1
Experimental
CC-5013
CC-5013 10 mg (two 5 mg capsules) daily on days 1-28 every 28 days (28 day cycles)