Efficacy and Safety of Adult Human Mesenchymal Stem Cells to Treat Steroid Refractory Acute Graft Versus Host Disease (GVHD)
Graft Versus Host Disease
About this trial
This is an interventional treatment trial for Graft Versus Host Disease focused on measuring Acute GVHD, Steroid refractory GVHD, Severe steroid refractory acute GVHD, Steroid refractory, Steroid Refractory Acute Graft Versus Host Disease
Eligibility Criteria
Inclusion Criteria: Participant must be 6 months to 70 years of age, inclusive. Participants who have failed to respond to steroid treatment. Failure to respond to steroid treatment is defined as any grade B-D (IBMTR) grading of acute GVHD that shows: No improvement after 3 days and a duration of no greater than 2 weeks while receiving treatment with methylprednisolone (greater than or equal to 1 mg/kg/day) or equivalent. Participant must be treated within 4 days of randomization. In urgent situations 2nd line therapy may be started 24 hours prior to randomization, and Prochymal® must be initiated within the following 3 days. Participants who have received an increase in their steroid dose treatment prior to randomization will be eligible for enrollment. An increase in steroid dose will not be considered as second line therapy. Participant must have adequate renal function as defined by: Calculated Creatinine Clearance of >30 milliliters per minute (mL/min) using the Cockcroft-Gault equation. For pediatric participants: Schwartz equation: (Participant population: infants over 1 week old through adolescence (<18 years old). Participants who are women of childbearing potential must be non-pregnant, not breast-feeding, and use adequate contraception. Male participants must use adequate contraception. Participant must have a minimum Karnofsky Performance Level of at least 30 at the time of study entry. Participant (or legal representative where appropriate) must be capable of providing written informed consent. Exclusion Criteria: Participant has started treatment with second line therapy >24 hours prior to randomization. Participant has received agents other than steroids for primary treatment of acute GVHD. Participant is participating in the CTN Protocol 0302. Participant has any underlying or current medical or psychiatric condition that, in the opinion of the Investigator, would interfere with the evaluation of the participant including uncontrolled infection, heart failure, pulmonary hypertension, etc. Participant may not receive any other investigational agents (not approved by the FDA) concurrently during study participation or within 30 days of randomization. Participant has a known allergy to bovine or porcine products. Participant has received a transplant for a solid tumor disease.
Sites / Locations
- University of Alabama at Birmingham
- Arizona Cancer Center
- City of Hope
- Univeristy of California San Francisco
- Yale New Haven Hospital
- University of Miami
- All Children's Hospital
- Emory University
- Northside Hospital
- Northwestern Center for Clinical Research
- Rush University Medical Center
- University of Illinois - Chicago
- Indiana Blood and Bone Marrow Transplant Center
- Univeristy of Iowa Hospitals and Clinics
- University of Kansas Medical Center
- University of Louisville
- Louisiana State University
- University of Maryland/Greenbaum
- Tufts-New England Medical Center
- Beth Israel Deaconess Medical Center
- Dana-Farber Cancer Institute
- Karmanos/Wayne State University
- Mayo Clinic Rochester
- Univeristy of Mississippi Medical Center
- University of Nebraska
- Hackensack University Medical Center
- Roswell Park
- New York Presbyterian Hospital
- Mount Sinai Medical Center
- Columbia University/New York Presbyterian Hospital
- University of Rochester
- New York Medical College
- Duke University
- Wake Forest Univeristy School of Medicine
- Oregon Health and Science University
- Penn State Hershey Medical Center
- Western Pennsylvania Cancer Institute
- Medical University of South Carolina
- Texas Cancer Center at Medical City
- Baylor University
- Univeristy of Texas Southwestern Medical Center
- MD Anderson Cancer Center
- Texas Research Center
- Virginia Commonwealth/Massey Cancer Center
- Fred Hutchinson Cancer Research Center
- University of Wisconsin Madison
- Medical College of Wisconsin
- Royal Brisbane Hospital
- Royal Melbourne Hospital
- Royal Perth Hospital
- Co-Medica Research Network
- British Columbia's Children's Hospital
- Cancer Care Manitoba
- Queen Elizabeth II Health Sciences Centre
- Hamilton Health Sciences Centre
- London Health Sciences Centre- Westminster Campus
- Ottawa Hospital
- Toronto General Hospital
- Princess Margaret Hospital
- Maisonneuve-Rosemont Hospital
- Hopital Enfant-Jesus
- Hopital du Saint-Sacrement
- Universia degli Studi di Pesaro
- IRCCS Policlinico San Matteo
- Kantonsspital Basel
- Barts & London School of Medicine
- John Radcliffe Hospital
- Bristol Royal Hospital for Children
- Glasgow Royal Infirmary
- Leeds General Infirmary
Arms of the Study
Arm 1
Arm 2
Active Comparator
Placebo Comparator
Prochymal®
Placebo
Participants who receive standard of care plus treatment with ex vivo cultured adult human mesenchymal stem cells.
Participants who receive standard of care and do not receive treatment with ex vivo cultured adult human mesenchymal stem cells.