Clinical Trial on the Use of Autologous Bone Marrow Stem Cells in Amyotrophic Lateral Sclerosis (CMN/ELA)
Primary Purpose
Amyotrophic Lateral Sclerosis
Status
Completed
Phase
Phase 1
Locations
Spain
Study Type
Interventional
Intervention
Laminectomy and bone marrow stem cells transplantation
Autologous bone marrow cells collection
Sponsored by
About this trial
This is an interventional treatment trial for Amyotrophic Lateral Sclerosis focused on measuring Amyotrophic Lateral Sclerosis, Bone marrow, Stem cells, Autologous, Safety
Eligibility Criteria
Inclusion Criteria:
- Diagnose established following the World Federation of Neurology criteria
- More than 6 and less than 36 months of evolution of the disease
- Medullar onset of the disease
- More than 20 and less than 65 years old
- Forced Vital Capacity equal or superior to 50%
- Total time of oxygen saturation <90% inferior to 2% of the sleeping time
- Signed informed consent
Exclusion Criteria:
- Neurological or psychiatric concomitant disease
- Need of parenteral or enteral nutrition through percutaneous endoscopic gastrostomy or nasogastric tube
- Concomitant systemic disease
- Treatment with corticosteroids, immunoglobulins or immunosuppressors during the last 12 months
- Inclusion in other clinical trials
- Unability to understand the informed consent
Sites / Locations
- Hospital Universitario Virgen de la Arrixaca
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
Transplant
Arm Description
T3-T4 laminectomy and bone marrow ficoll separated mononuclear autologous cells intraspinal transplantation
Outcomes
Primary Outcome Measures
Forced vital capacity
Secondary Outcome Measures
ALS-FRS, MRC and Norris scales
Absence of adverse events
Full Information
NCT ID
NCT00855400
First Posted
March 3, 2009
Last Updated
December 1, 2010
Sponsor
Fundacion para la Formacion e Investigacion Sanitarias de la Region de Murcia
Collaborators
Carlos III Health Institute, Hospital Universitario Virgen de la Arrixaca, Hospital General Universitario Morales Meseguer, Diógenes Foundation
1. Study Identification
Unique Protocol Identification Number
NCT00855400
Brief Title
Clinical Trial on the Use of Autologous Bone Marrow Stem Cells in Amyotrophic Lateral Sclerosis
Acronym
CMN/ELA
Official Title
Phase I/II Clinical Trial on the Use of Autologous Bone Marrow Stem Cells in Amyotrophic Lateral Sclerosis
Study Type
Interventional
2. Study Status
Record Verification Date
December 2010
Overall Recruitment Status
Completed
Study Start Date
February 2007 (undefined)
Primary Completion Date
October 2009 (Actual)
Study Completion Date
February 2010 (Actual)
3. Sponsor/Collaborators
Name of the Sponsor
Fundacion para la Formacion e Investigacion Sanitarias de la Region de Murcia
Collaborators
Carlos III Health Institute, Hospital Universitario Virgen de la Arrixaca, Hospital General Universitario Morales Meseguer, Diógenes Foundation
4. Oversight
Data Monitoring Committee
Yes
5. Study Description
Brief Summary
The purpose of this clinical trial is to asses the feasibility and the security of the intraspinal infusion of autologous bone marrow stem cells for the treatment of Amyotrophic Lateral Sclerosis patients.
Detailed Description
Patients with Amyotrophic Lateral Sclerosis (ALS) typically endure a progressive paralysis due to the continued loss of motoneurons that leads them to death in less than 5 years. No treatment has changed its natural history. Intraspinal injections of bone marrow mononuclear cells (MNC) have been able to ameliorate the course of ALS in murine models, acting as pumps of trophic factors that keep the motoneurons functional. We have designed a phase I/II clinical trial to check the feasibility of this approach in humans.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Amyotrophic Lateral Sclerosis
Keywords
Amyotrophic Lateral Sclerosis, Bone marrow, Stem cells, Autologous, Safety
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 1, Phase 2
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
Non-Randomized
Enrollment
11 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Transplant
Arm Type
Experimental
Arm Description
T3-T4 laminectomy and bone marrow ficoll separated mononuclear autologous cells intraspinal transplantation
Intervention Type
Procedure
Intervention Name(s)
Laminectomy and bone marrow stem cells transplantation
Intervention Description
T3-T4 laminectomy and bone marrow ficoll separated mononuclear autologous cells intraspinal transplantation
Intervention Type
Procedure
Intervention Name(s)
Autologous bone marrow cells collection
Intervention Description
Autologous bone marrow cells collection under sedation. Sixty mL are obtained and processed through a ficoll gradient.
Primary Outcome Measure Information:
Title
Forced vital capacity
Time Frame
Every 3 months
Secondary Outcome Measure Information:
Title
ALS-FRS, MRC and Norris scales
Time Frame
Every 3 months
Title
Absence of adverse events
Time Frame
Every week / month depending on the study phase
10. Eligibility
Sex
All
Minimum Age & Unit of Time
20 Years
Maximum Age & Unit of Time
65 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Diagnose established following the World Federation of Neurology criteria
More than 6 and less than 36 months of evolution of the disease
Medullar onset of the disease
More than 20 and less than 65 years old
Forced Vital Capacity equal or superior to 50%
Total time of oxygen saturation <90% inferior to 2% of the sleeping time
Signed informed consent
Exclusion Criteria:
Neurological or psychiatric concomitant disease
Need of parenteral or enteral nutrition through percutaneous endoscopic gastrostomy or nasogastric tube
Concomitant systemic disease
Treatment with corticosteroids, immunoglobulins or immunosuppressors during the last 12 months
Inclusion in other clinical trials
Unability to understand the informed consent
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Jose Maria Moraleda Jiménez, M.D. Ph.D.
Organizational Affiliation
Hospital Universitario Virgen de la Arrixaca
Official's Role
Study Director
Facility Information:
Facility Name
Hospital Universitario Virgen de la Arrixaca
City
El Palmar
State/Province
Murcia
ZIP/Postal Code
30120
Country
Spain
12. IPD Sharing Statement
Citations:
PubMed Identifier
22415951
Citation
Blanquer M, Moraleda JM, Iniesta F, Gomez-Espuch J, Meca-Lallana J, Villaverde R, Perez-Espejo MA, Ruiz-Lopez FJ, Garcia Santos JM, Bleda P, Izura V, Saez M, De Mingo P, Vivancos L, Carles R, Jimenez J, Hernandez J, Guardiola J, Del Rio ST, Antunez C, De la Rosa P, Majado MJ, Sanchez-Salinas A, Lopez J, Martinez-Lage JF, Martinez S. Neurotrophic bone marrow cellular nests prevent spinal motoneuron degeneration in amyotrophic lateral sclerosis patients: a pilot safety study. Stem Cells. 2012 Jun;30(6):1277-85. doi: 10.1002/stem.1080.
Results Reference
derived
Learn more about this trial
Clinical Trial on the Use of Autologous Bone Marrow Stem Cells in Amyotrophic Lateral Sclerosis
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