Trial to Evaluate the Efficacy and Safety of a New Full Length Recombinant Human FVIII for Hemophilia A (Leopold I)
Blood Coagulation Disorders, Hemophilia A
About this trial
This is an interventional treatment trial for Blood Coagulation Disorders focused on measuring Hemophilia A, Factor VIII, Prophylaxis
Eligibility Criteria
Inclusion Criteria:
- Male, aged 12 to 65 years
- Severe hemophilia A defined as < 1% FVIII:C
- >/= 150 days of previous treatment with FVIII in lifetime
- Currently receiving on-demand or any type of prophylaxis treatment regimen with any FVIII product
- No history of or current FVIII inhibitors
Exclusion Criteria:
- Presence of another bleeding disease that is different from hemophilia A (e.g., von Willebrand disease, hemophilia B)
- Low platelet count, abnormal kidney function, or liver disease
- Received treatment with immune suppressing drugs within the last 3 months prior or requires treatment during the study. (Some drugs for hepatitis C, Human immunodeficiency virus (HIV), and steroids are allowed)
- Receiving or has received other experimental drugs within 3 months prior to study entry
- Allergy to Factor VIII or hamsters or mouse protein
Sites / Locations
- Karolinska Universitetssjukhuset i Solna
Arms of the Study
Arm 1
Arm 2
Arm 3
Arm 4
Arm 5
Experimental
Experimental
Experimental
Experimental
Experimental
Arm 1: Recombinant Factor VIII (BAY81-8973) then Kogenate FS
Arm 2: Kogenate FS then Recombinant Factor VIII (BAY81-8973)
Arm 3: Recombinant Factor VIII by CS/EP then by CS/ADJ
Arm 4: Recombinant Factor VIII by CS/ADJ then by CS/EP
Arm 5: Recombinant Factor VIII by CS/EP
Part A - Arm 1: Participants first received one single intravenous (IV) injection of BAY81-8973 50 IU/kg, then 1 single IV injection of Kogenate FS (BAY14-2222) 50 IU/kg with a wash-out period of at least 2-3 days in between
Part A - Arm 2: Participants first received one single intravenous (IV) injection of Kogenate FS (BAY14-2222) 50 IU/kg, then 1 single IV injection of BAY81-8973 50 IU/kg with a wash-out period of at least 2-3 days in between
Part B - Arm 3: Participants received IV injection of BAY81-8973 at 20-50 IU/kg 2-3 times per week with BAY81-8973 measured by Chromogenic Substrate Assay Potency Per European Pharmacopeia for 6 months and then crossed over to study drug measured by Chromogenic Substrate Assay/Adjusted to Label Potency for 6 months
Part B - Arm 4:. Participants received IV injection of BAY81-8973 at 20-50 IU/kg 2-3 times per week with BAY81-8973 measured by Chromogenic Substrate Assay/Adjusted to Label Potency for 6 months and then crossed over to study drug measured by Chromogenic Substrate Assay Per European Pharmacopeia for 6 months
Part C - Arm 5: Participants received a loading dose of approximately 50 IU/kg of BAY 81-8973 before the first surgical incision followed by further treatment with BAY 81-8973 according to surgical requirements for up to 3 weeks