Characterization Phenotypic and Genetic Study of the Intestinal Epithelial Dysplasia or Tufting Enteropathy (TE) (DEI)
Primary Purpose
Intestinal Epithelial Dysplasia, Tufting Enteropathy
Status
Completed
Phase
Not Applicable
Locations
France
Study Type
Interventional
Intervention
blood samples and skin biopsies
Skin biopsies
Sponsored by
About this trial
This is an interventional diagnostic trial for Intestinal Epithelial Dysplasia focused on measuring intestinal epithelial dysplasia, characterization phenotypic, genetic study, or " tufting enteropathy "
Eligibility Criteria
Inclusion criteria :
Patient sent in the service of Gastroenterology Pediatric Hepatology of the Hospital Necker Enfants Malades for an intestinal transplantation, from 0 to 15 years old presenting:
- A known epithelial dysplasia (Diagnosis established on the clinical and histo-morphological criteria from one or several intestinal biopsies, with or without diagnosis known or suspected in the family). The objectives are the phenotypic characterization of the case and the revealing of markers characteristic immuno-histochemistry which can be of use to the diagnosis and direct to candidate genes
- Or a suspicion of dysplasia epithelial (compatible clinical History(Story) with or without extra-digestive demonstrations(appearances) of type keratinate punctuated superficial (KPS), abnormalities cutanea or atresia CHOANS with atypical digestive histology and without diagnosis known in the family). The objectives are the diagnosis on the basis of the immuno-histochemistry expression and the existence of an infringement(achievement) conjunctival and the phenotypic characterization of the case
- The lit(enlightened) and written consent of both holders of the parental authority must be beforehand obtained as well as that of the patient if it is in age to understand(include).
Exclusion criteria :
- Not membership in a national insurance scheme (beneficiary or legal successor)
- Family not understanding(including) French
- Refusal of one of both relatives(parents)
Sites / Locations
- Necker Hospital
Arms of the Study
Arm 1
Arm 2
Arm Type
Experimental
Other
Arm Label
Patients
Control
Arm Description
intestinal epithelial dysplasia
Children without intestinal epithelial dysplasia
Outcomes
Primary Outcome Measures
gene identification
identification of different family of genes involved in intestinal dysplasia
Secondary Outcome Measures
mutation identification
Identification of different mutations involved in intestinal dysplasia
Full Information
NCT ID
NCT01114035
First Posted
April 29, 2010
Last Updated
August 1, 2013
Sponsor
Assistance Publique - Hôpitaux de Paris
1. Study Identification
Unique Protocol Identification Number
NCT01114035
Brief Title
Characterization Phenotypic and Genetic Study of the Intestinal Epithelial Dysplasia or Tufting Enteropathy (TE)
Acronym
DEI
Official Title
Characterization Phenotypic and Genetic Study of the Intestinal Epithelial Dysplasia or TE
Study Type
Interventional
2. Study Status
Record Verification Date
August 2013
Overall Recruitment Status
Completed
Study Start Date
April 2010 (undefined)
Primary Completion Date
April 2013 (Actual)
Study Completion Date
July 2013 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Assistance Publique - Hôpitaux de Paris
4. Oversight
Data Monitoring Committee
No
5. Study Description
Brief Summary
This PHRC is centred on the intestinal epithelial dysplasia ( DEI) or " tufting enteropathy " or TE the clinical and histo-pathological descriptions of which are specified well to the digestive plan(shot).
Detailed Description
The objectives of this PHRC are:
the phenotypic analysis of the intestinal epithelial dysplasia by clinical and histo-pathological investigations.
the identification of proteins involved at the intestinal level in the differentiation, the proliferation and the membership of the epithelial cells
from the phenotypic study, a genetic analysis of type maps by homozygote on the whole genome partner in an approach guided by possible candidate genes
the study of the genes, chosen according to their location, to their profile of expression, and to their function in touch with the pathogenic hypotheses
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Intestinal Epithelial Dysplasia, Tufting Enteropathy
Keywords
intestinal epithelial dysplasia, characterization phenotypic, genetic study, or " tufting enteropathy "
7. Study Design
Primary Purpose
Diagnostic
Study Phase
Not Applicable
Interventional Study Model
Parallel Assignment
Masking
None (Open Label)
Allocation
Non-Randomized
Enrollment
41 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Patients
Arm Type
Experimental
Arm Description
intestinal epithelial dysplasia
Arm Title
Control
Arm Type
Other
Arm Description
Children without intestinal epithelial dysplasia
Intervention Type
Genetic
Intervention Name(s)
blood samples and skin biopsies
Intervention Description
to detect mutations
Intervention Type
Genetic
Intervention Name(s)
Skin biopsies
Other Intervention Name(s)
to detect mutations
Intervention Description
to detect mutations
Primary Outcome Measure Information:
Title
gene identification
Description
identification of different family of genes involved in intestinal dysplasia
Time Frame
6 months
Secondary Outcome Measure Information:
Title
mutation identification
Description
Identification of different mutations involved in intestinal dysplasia
Time Frame
6 months
10. Eligibility
Sex
All
Maximum Age & Unit of Time
15 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion criteria :
Patient sent in the service of Gastroenterology Pediatric Hepatology of the Hospital Necker Enfants Malades for an intestinal transplantation, from 0 to 15 years old presenting:
A known epithelial dysplasia (Diagnosis established on the clinical and histo-morphological criteria from one or several intestinal biopsies, with or without diagnosis known or suspected in the family). The objectives are the phenotypic characterization of the case and the revealing of markers characteristic immuno-histochemistry which can be of use to the diagnosis and direct to candidate genes
Or a suspicion of dysplasia epithelial (compatible clinical History(Story) with or without extra-digestive demonstrations(appearances) of type keratinate punctuated superficial (KPS), abnormalities cutanea or atresia CHOANS with atypical digestive histology and without diagnosis known in the family). The objectives are the diagnosis on the basis of the immuno-histochemistry expression and the existence of an infringement(achievement) conjunctival and the phenotypic characterization of the case
The lit(enlightened) and written consent of both holders of the parental authority must be beforehand obtained as well as that of the patient if it is in age to understand(include).
Exclusion criteria :
Not membership in a national insurance scheme (beneficiary or legal successor)
Family not understanding(including) French
Refusal of one of both relatives(parents)
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Olivier Goulet, MD, PhD
Organizational Affiliation
Assistance Publique - Hôpitaux de Paris
Official's Role
Principal Investigator
Facility Information:
Facility Name
Necker Hospital
City
Paris
ZIP/Postal Code
75015
Country
France
12. IPD Sharing Statement
Learn more about this trial
Characterization Phenotypic and Genetic Study of the Intestinal Epithelial Dysplasia or Tufting Enteropathy (TE)
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