A Multiple Dose Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Romosozumab (AMG 785)
Primary Purpose
Postmenopausal, Osteopenia
Status
Completed
Phase
Phase 1
Locations
Study Type
Interventional
Intervention
Romosozumab
Placebo
Sponsored by
About this trial
This is an interventional treatment trial for Postmenopausal
Eligibility Criteria
Inclusion Criteria:
- Healthy males and females between 45 to 80 years of age
- Postmenopausal females
- Low bone mineral density, defined by bone mineral density (BMD) T-scores between -1.0 and -2.5, inclusive, for the lumbar spine [L1-L4] or total evaluable vertebrae [if fewer than L1-L4] or total hip)
- 25-hydroxyvitamin D ≥ 20 ng/mL
- Weight ≤ 98 kg (216 lb) and/or height ≤ 196 cm (77 in)
Exclusion Criteria:
- Osteoporosis defined by bone mineral density (BMD) T-scores < -2.5 for the lumbar spine (L1-L4) or total evaluable vertebrae (if fewer than L1-L4) or total hip
- Diagnosed with any condition that would affect bone metabolism
- Previous exposure to AMG 785
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm Type
Placebo Comparator
Experimental
Arm Label
Placebo
Romosozumab
Arm Description
Participants were randomized to receive matching placebo administered by subcutaneous injection once every 2 weeks (Q2W) or once every 4 weeks (Q4W) for 3 months.
Participants were randomized to receive romosozumab administered by subcutaneous injection at doses of 1 mg/kg Q2W, 2 mg/kg Q4W, 2 mg/kg Q2W, or 3 mg/kg Q4W for 3 months.
Outcomes
Primary Outcome Measures
Number of Participants With Adverse Events
Serious adverse events were any events that were fatal, were life-threatening (placed the participant at immediate risk of death), required in-patient hospitalization or prolongation of existing hospitalization, resulted in persistent or significant disability/incapacity, were congenital anomalies or birth defects, or were other significant medical hazards.
Relatedness to investigational product was assessed by the investigator by means of the question: "Is there a reasonable possibility that the event may have been caused by the investigational product?'
Number of Participants Who Developed Antibodies to Romosozumab
All samples were tested for binding anti-romsozumab antibodies using an immunoassay; all antibody-positive samples were further tested in a bioassay to determine if the antibodies were neutralizing.
Development of antibodies to romosozumab is defined as participants with a negative result at baseline and a positive result at any time postbaseline.
Secondary Outcome Measures
Time to Maximum Observed Concentration (Tmax) of Romosozumab
Serum concentrations of romosozumab were measured by a validated enzyme-linked immunosorbent assay; the lower limit of quantification (LLOQ) was 50 ng/mL.
Maximum Observed Concentration (Cmax) of Romosozumab
Area Under the Concentration-time Curve for the Dosing Interval (AUC0-tau) for Romosozumab
Area under the serum romosozumab concentration-time curve from time 0 to tau (tau = 14 days for Q2W dose cohorts and 28 days for Q4W dose cohorts)
Half-life Associated With the Terminal Phase of Elimination (T1/2) for Romosozumab
Accumulation Ratio (AR) for Romosozumab
The accumulation ratio (AR) was calculated as the ratio of AUC0-tau after the last dose to AUC0-tau after the first dose.
Percent Change From Baseline in Bone Mineral Density of the Total Spine
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans of the lumbar spine (L1-L4) and assessed by a central lab.
Percent Change From Baseline in Bone Mineral Density at the Total Hip
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Percent Change From Baseline in Bone Mineral Density at the Femoral Hip
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Percent Change From Baseline in Bone Mineral Density at the Distal One-third Radius
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Percent Change From Baseline in Bone Mineral Density at the Total Wrist
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Percent Change From Baseline in Bone Mineral Density of the Whole Body
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Percent Change From Baseline in Procollagen Type 1 N-terminal Propeptide (P1NP)
Percent Change From Baseline in Osteocalcin
Percent Change From Baseline in Bone-specific Alkaline Phosphatase (BSAP)
Percent Change From Baseline in Serum C-telopeptide (sCTX)
Percent Change From Baseline in Intact Parathyroid Hormone (iPTH)
Percent Change From Baseline in Sclerostin
Change From Baseline in Ionized Calcium
Full Information
1. Study Identification
Unique Protocol Identification Number
NCT01825785
Brief Title
A Multiple Dose Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Romosozumab (AMG 785)
Official Title
A Randomized, Double-blind, Placebo-controlled, Ascending Multiple Dose Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of AMG 785 in Healthy Men and Postmenopausal Women With Low Bone Mass
Study Type
Interventional
2. Study Status
Record Verification Date
April 2019
Overall Recruitment Status
Completed
Study Start Date
November 14, 2007 (Actual)
Primary Completion Date
December 2, 2008 (Actual)
Study Completion Date
December 2, 2008 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Amgen
4. Oversight
Data Monitoring Committee
No
5. Study Description
Brief Summary
The primary objective of this study was to assess the safety, tolerability, and immunogenicity potential of romosozumab following multiple subcutaneous (SC) administrations in healthy men and postmenopausal women with low bone mass.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Postmenopausal, Osteopenia
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 1
Interventional Study Model
Sequential Assignment
Masking
ParticipantInvestigator
Allocation
Randomized
Enrollment
48 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Placebo
Arm Type
Placebo Comparator
Arm Description
Participants were randomized to receive matching placebo administered by subcutaneous injection once every 2 weeks (Q2W) or once every 4 weeks (Q4W) for 3 months.
Arm Title
Romosozumab
Arm Type
Experimental
Arm Description
Participants were randomized to receive romosozumab administered by subcutaneous injection at doses of 1 mg/kg Q2W, 2 mg/kg Q4W, 2 mg/kg Q2W, or 3 mg/kg Q4W for 3 months.
Intervention Type
Drug
Intervention Name(s)
Romosozumab
Other Intervention Name(s)
AMG 785, EVENITY™
Intervention Description
Administered by subcutaneous injection
Intervention Type
Drug
Intervention Name(s)
Placebo
Intervention Description
Administered by subcutaneous injection
Primary Outcome Measure Information:
Title
Number of Participants With Adverse Events
Description
Serious adverse events were any events that were fatal, were life-threatening (placed the participant at immediate risk of death), required in-patient hospitalization or prolongation of existing hospitalization, resulted in persistent or significant disability/incapacity, were congenital anomalies or birth defects, or were other significant medical hazards.
Relatedness to investigational product was assessed by the investigator by means of the question: "Is there a reasonable possibility that the event may have been caused by the investigational product?'
Time Frame
169 days
Title
Number of Participants Who Developed Antibodies to Romosozumab
Description
All samples were tested for binding anti-romsozumab antibodies using an immunoassay; all antibody-positive samples were further tested in a bioassay to determine if the antibodies were neutralizing.
Development of antibodies to romosozumab is defined as participants with a negative result at baseline and a positive result at any time postbaseline.
Time Frame
Blood samples for detection of anti-romosozumab antibodies were collected at day 1 (predose) and days 29 (predose), 57 (predose), 85, 113, 141, and 169.
Secondary Outcome Measure Information:
Title
Time to Maximum Observed Concentration (Tmax) of Romosozumab
Description
Serum concentrations of romosozumab were measured by a validated enzyme-linked immunosorbent assay; the lower limit of quantification (LLOQ) was 50 ng/mL.
Time Frame
Q2W dose groups: First dose on days 1 (predose) to 15 (predose); Last dose on days 71 (predose) to 169. Q4W dose groups: First dose on days 1 (predose) to 29 (predose); Last dose on days 57 (predose) to 169.
Title
Maximum Observed Concentration (Cmax) of Romosozumab
Time Frame
Q2W dose groups: First dose on days 1 (predose) to 15 (predose); Last dose on days 71 (predose) to 169. Q4W dose groups: First dose on days 1 (predose) to 29 (predose); Last dose on days 57 (predose) to 169.
Title
Area Under the Concentration-time Curve for the Dosing Interval (AUC0-tau) for Romosozumab
Description
Area under the serum romosozumab concentration-time curve from time 0 to tau (tau = 14 days for Q2W dose cohorts and 28 days for Q4W dose cohorts)
Time Frame
Q2W dose groups: First dose on days 1 (predose) to 15 (predose); Last dose on days 71 (predose) to 169. Q4W dose groups: First dose on days 1 (predose) to 29 (predose); Last dose on days 57 (predose) to 169.
Title
Half-life Associated With the Terminal Phase of Elimination (T1/2) for Romosozumab
Time Frame
Q2W dose groups: days 71 (predose) to 169; Q24 dose groups: days 57 (predose) to 169.
Title
Accumulation Ratio (AR) for Romosozumab
Description
The accumulation ratio (AR) was calculated as the ratio of AUC0-tau after the last dose to AUC0-tau after the first dose.
Time Frame
Q2W dose groups: First dose on days 1 (predose) to 15 (predose); Last dose on days 71 (predose) to 169. Q4W dose groups: First dose on days 1 (predose) to 29 (predose); Last dose on days 57 (predose) to 169.
Title
Percent Change From Baseline in Bone Mineral Density of the Total Spine
Description
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans of the lumbar spine (L1-L4) and assessed by a central lab.
Time Frame
Baseline and days 29, 85, 127, and 169
Title
Percent Change From Baseline in Bone Mineral Density at the Total Hip
Description
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Time Frame
Baseline and days 29, 85, 127, and 169
Title
Percent Change From Baseline in Bone Mineral Density at the Femoral Hip
Description
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Time Frame
Baseline and days 29, 85, 127, and 169
Title
Percent Change From Baseline in Bone Mineral Density at the Distal One-third Radius
Description
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Time Frame
Baseline and days 29, 85, 127, and 169
Title
Percent Change From Baseline in Bone Mineral Density at the Total Wrist
Description
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Time Frame
Baseline and days 29, 85, 127, and 169
Title
Percent Change From Baseline in Bone Mineral Density of the Whole Body
Description
Bone mineral density was determined by dual energy X-ray absorptiometry (DXA) scans and assessed by a central lab.
Time Frame
Baseline and days 29, 85, 127, and 169
Title
Percent Change From Baseline in Procollagen Type 1 N-terminal Propeptide (P1NP)
Time Frame
Baseline and days 2, 4, 6, 8, 15, 22, 29, 36, 43, 50 (Q2W only), 57, 58 (Q4W only), 60 (Q4W only), 62 (Q4W only), 64, 71, 72 (Q2W only), 74 (Q2W only), 76 (Q2W only), 78, 85, 99, 113, 127, 141, 155 and 169
Title
Percent Change From Baseline in Osteocalcin
Time Frame
Baseline and days 2, 4, 6, 8, 15, 22, 29, 36, 43, 50 (Q2W only), 57, 58 (Q4W only), 60 (Q4W only), 62 (Q4W only), 64, 71, 72 (Q2W only), 74 (Q2W only), 76 (Q2W only), 78, 85, 99, 113, 127, 141, 155 and 169
Title
Percent Change From Baseline in Bone-specific Alkaline Phosphatase (BSAP)
Time Frame
Baseline and days 2, 4, 6, 8, 15, 22, 29, 36, 43, 50 (Q2W only), 57, 58 (Q4W only), 60 (Q4W only), 62 (Q4W only), 64, 71, 72 (Q2W only), 74 (Q2W only), 76 (Q2W only), 78, 85, 99, 113, 127, 141, 155 and 169
Title
Percent Change From Baseline in Serum C-telopeptide (sCTX)
Time Frame
Baseline and days 2, 4, 6, 8, 15, 22, 29, 36, 43, 50 (Q2W only), 57, 58 (Q4W only), 60 (Q4W only), 62 (Q4W only), 64, 71, 72 (Q2W only), 74 (Q2W only), 76 (Q2W only), 78, 85, 99, 113, 127, 141, 155 and 169
Title
Percent Change From Baseline in Intact Parathyroid Hormone (iPTH)
Time Frame
Baseline and days 2, 4, 6, 8, 15, 22, 29, 36, 43, 50 (Q2W only), 57, 58 (Q4W only), 60 (Q4W only), 62 (Q4W only), 64, 71, 72 (Q2W only), 74 (Q2W only), 76 (Q2W only), 78, 85, 99, 113, 127, 141, 155 and 169
Title
Percent Change From Baseline in Sclerostin
Time Frame
Baseline and days 15, 29, 43, 57, 71, 85, 99, 113, 127, 141, 155 and 169
Title
Change From Baseline in Ionized Calcium
Time Frame
Baseline and day 169 (or earlier for participants who discontinued before day 169)
10. Eligibility
Sex
All
Minimum Age & Unit of Time
45 Years
Maximum Age & Unit of Time
80 Years
Accepts Healthy Volunteers
Accepts Healthy Volunteers
Eligibility Criteria
Inclusion Criteria:
Healthy males and females between 45 to 80 years of age
Postmenopausal females
Low bone mineral density, defined by bone mineral density (BMD) T-scores between -1.0 and -2.5, inclusive, for the lumbar spine [L1-L4] or total evaluable vertebrae [if fewer than L1-L4] or total hip)
25-hydroxyvitamin D ≥ 20 ng/mL
Weight ≤ 98 kg (216 lb) and/or height ≤ 196 cm (77 in)
Exclusion Criteria:
Osteoporosis defined by bone mineral density (BMD) T-scores < -2.5 for the lumbar spine (L1-L4) or total evaluable vertebrae (if fewer than L1-L4) or total hip
Diagnosed with any condition that would affect bone metabolism
Previous exposure to AMG 785
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
MD
Organizational Affiliation
Amgen
Official's Role
Study Director
12. IPD Sharing Statement
Links:
URL
http://www.amgentrials.com
Description
AmgenTrials clinical trials website
Learn more about this trial
A Multiple Dose Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Romosozumab (AMG 785)
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