Safety of Post-transplant Alpha-beta Depleted T-cell Infusion Following Haploidentical Stem Cell Transplant (Haplo SCT) (ABD)
Primary Purpose
Hematologic Neoplasms, Graft-Versus-Host Disease
Status
Completed
Phase
Not Applicable
Locations
United States
Study Type
Interventional
Intervention
Alpha-beta depleted T-cell infusion after post-transplant cyclophosphamide.
Sponsored by
About this trial
This is an interventional treatment trial for Hematologic Neoplasms focused on measuring stem cell transplant
Eligibility Criteria
Inclusion Criteria:
- Neoplastic hematological disorder with indication of allogeneic transplant
- No available suitable HLA-matched donor
- Adequate cardiac, pulmonary, renal, and hepatic function
- Karnofsky performance status score greater than or equal to 70%
Exclusion Criteria:
- Medication non-compliance
- No appropriate caregiver identified
- Uncontrolled medical or psychiatric disorder
- Active central nervous system (CNS) neoplastic involvement
- Known allergy to Dimethyl Sulfoxide
- HIV1 or HIV2 positive
- Pregnant or breastfeeding
Sites / Locations
- UAB Medical Center (University of Alabama at Birmingham)
Arms of the Study
Arm 1
Arm Type
Other
Arm Label
Alpha-beta depleted T-cell infusion
Arm Description
Post-transplant alpha-beta depleted T-cell infusion after post-transplant cyclophosphamide.
Outcomes
Primary Outcome Measures
Number of Participants That Experience Acute Haploidentical Alpha Beta Depleted Transplant (aGVHD)
Patients will be monitored for Grade IV aGVHD and organ toxicity. Acute assessment will be done using the modified Keystone (Glucksberg) consensus criteria.
Number of Participants That Experience Chronic Haploidentical Alpha Beta Depleted Transplant (cGVHD)
Patients will be monitored for Grade IV cGVHD and organ toxicity. Chronic assessment will be done using the conventional criteria.
Secondary Outcome Measures
Full Information
1. Study Identification
Unique Protocol Identification Number
NCT02193880
Brief Title
Safety of Post-transplant Alpha-beta Depleted T-cell Infusion Following Haploidentical Stem Cell Transplant (Haplo SCT)
Acronym
ABD
Official Title
Safety of Post-transplant Alpha-beta Depleted T-cell Infusion Following Haploidentical Stem Cell Transplant (Haplo SCT)
Study Type
Interventional
2. Study Status
Record Verification Date
April 2019
Overall Recruitment Status
Completed
Study Start Date
October 9, 2014 (Actual)
Primary Completion Date
March 13, 2018 (Actual)
Study Completion Date
March 13, 2018 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor-Investigator
Name of the Sponsor
Ayman Saad
4. Oversight
Studies a U.S. FDA-regulated Drug Product
No
Studies a U.S. FDA-regulated Device Product
Yes
Device Product Not Approved or Cleared by U.S. FDA
Yes
Data Monitoring Committee
Yes
5. Study Description
Brief Summary
The purpose of this study is to determine the safety and efficacy of post-transplant cyclophosphamide and a post-transplant infusion of donor cells, that have been specially processed to remove alpha beta t-cells, in patients undergoing a haploidentical allogeneic stem cell transplant to help reduce the risk of relapse without increasing the risk of graft-versus-host disease.
Detailed Description
Transplant patients participating in this clinical trial will receive one of 3 standard pre-transplant chemotherapy preparative regimens as appropriate for their specific disease. They will then receive a standard non-manipulated donor stem cell infusion on transplant day (day 0) followed by cyclophosphamide (days +3 and +4) and an alpha-beta t-cell reduced donor stem cell infusion on day +7.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Hematologic Neoplasms, Graft-Versus-Host Disease
Keywords
stem cell transplant
7. Study Design
Primary Purpose
Treatment
Study Phase
Not Applicable
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
7 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Alpha-beta depleted T-cell infusion
Arm Type
Other
Arm Description
Post-transplant alpha-beta depleted T-cell infusion after post-transplant cyclophosphamide.
Intervention Type
Device
Intervention Name(s)
Alpha-beta depleted T-cell infusion after post-transplant cyclophosphamide.
Intervention Description
Post-transplant alpha-beta depleted T-cell infusion after post-transplant cyclophosphamide.
Primary Outcome Measure Information:
Title
Number of Participants That Experience Acute Haploidentical Alpha Beta Depleted Transplant (aGVHD)
Description
Patients will be monitored for Grade IV aGVHD and organ toxicity. Acute assessment will be done using the modified Keystone (Glucksberg) consensus criteria.
Time Frame
From baseline and before day +100 of transplant.
Title
Number of Participants That Experience Chronic Haploidentical Alpha Beta Depleted Transplant (cGVHD)
Description
Patients will be monitored for Grade IV cGVHD and organ toxicity. Chronic assessment will be done using the conventional criteria.
Time Frame
From baseline and before day +100 of transplant.
10. Eligibility
Sex
All
Minimum Age & Unit of Time
19 Years
Maximum Age & Unit of Time
65 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Neoplastic hematological disorder with indication of allogeneic transplant
No available suitable HLA-matched donor
Adequate cardiac, pulmonary, renal, and hepatic function
Karnofsky performance status score greater than or equal to 70%
Exclusion Criteria:
Medication non-compliance
No appropriate caregiver identified
Uncontrolled medical or psychiatric disorder
Active central nervous system (CNS) neoplastic involvement
Known allergy to Dimethyl Sulfoxide
HIV1 or HIV2 positive
Pregnant or breastfeeding
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Ayman Saad, MD
Organizational Affiliation
University of Alabama at Birmingham
Official's Role
Principal Investigator
Facility Information:
Facility Name
UAB Medical Center (University of Alabama at Birmingham)
City
Birmingham
State/Province
Alabama
ZIP/Postal Code
35233
Country
United States
12. IPD Sharing Statement
Plan to Share IPD
No
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Links:
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Learn more about this trial
Safety of Post-transplant Alpha-beta Depleted T-cell Infusion Following Haploidentical Stem Cell Transplant (Haplo SCT)
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