LME636 in the Relief of Persistent Ocular Discomfort in Subjects With Severe Dry Eye Disease
Primary Purpose
Dry Eye
Status
Completed
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
LME636 ophthalmic solution
LME636 Vehicle
Sponsored by
About this trial
This is an interventional treatment trial for Dry Eye focused on measuring LME636, dry eye disease, efficacy, ocular discomfort
Eligibility Criteria
Inclusion Criteria:
- Must sign written informed consent.
- Physician diagnosis of DED of at least 6 months prior to Visit 1.
- Must use artificial tears, gels, lubricants or re-wetting drops on a regular basis.
- Respond as "often" or "constantly" to the question "How often do your eyes feel uncomfortable?".
- Best Corrected Visual Acuity (BCVA) of 55 or greater in each eye as measured by ETDRS at Visit 1.
- Other protocol-specified inclusion criteria may apply.
Exclusion Criteria:
- Presence of any acute infection or non-infectious ocular condition in either eye within 1 month of Visit 1.
- Contact lens wearers, defined as individuals who cannot be without their contact lenses for the entire duration of the study.
- Any chronic ocular degenerative condition that in the opinion of the Investigator could possibly advance during the time course of the study.
- Use of biologics treatments, such as systemic biologic anti-cytokines, including anti-TNFα drugs, or immunosuppressive therapy for the treatment of severe systemic autoimmune disorders.
- Diseases or conditions affecting the ocular surface that are associated with clinically significant scarring and or destruction of conjunctiva and/or cornea.
- Unwilling to abstain from topical ocular non-prescription medications during the course of the study, including concomitant use of artificial tears, gels, lubricants, re-wetting drops, allergy drops, etc. after Visit 2.
- Use of nasal, inhaled, systemic (including injections), or topical corticosteroids within 30 days of Visit 1.
- Women of child-bearing potential unwilling to use effective contraception methods as defined in the protocol.
- Other protocol-specified exclusion criteria may apply.
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm Type
Experimental
Placebo Comparator
Arm Label
LME636
Vehicle
Arm Description
LME636 ophthalmic solution, 1 drop (approx. 40 µL; 2.4 mg) administered topically in each eye 3 times a day (TID) for 6 weeks
LME636 Vehicle, 1 drop administered topically in each eye TID for 6 weeks
Outcomes
Primary Outcome Measures
Mean Change From Baseline in Global Ocular Discomfort Score at Day 71
Discomfort frequency and severity (each graded on a separate 100-units scale) were assessed daily using a visual analog scale (VAS) displayed on a handheld digital Pad (electronic patient-reported outcome (ePRO)). Frequency score was in response to the question 'how often your eyes felt uncomfortable during the past 24 hours' ranging from 'Rarely' to 'All the time.' Severity score was in response to the question 'how uncomfortable your eyes felt during the past 24 hours' ranging from 'Very mildly uncomfortable' to 'Very severely uncomfortable.' The Global Ocular Discomfort Score, ranging from 0 to 100, was calculated for any given day, as the square root of the product of the discomfort frequency score multiplied by the discomfort severity score. Improvement results in a reduction of the discomfort frequency or severity, or both, translating into a reduction of the resulting Global Ocular Discomfort score as compared to baseline. A negative change from baseline indicates improvement.
Best Corrected Visual Acuity (BCVA)
Visual Acuity (VA) with the subject's best spectacles or other visual corrective devices was measured using an ETDRS visual acuity chart at 3 meters (10 feet) and reported in letters read correctly. An increase (gain) in letters read indicates improvement. Both eyes contributed to the analysis.
Intraocular Pressure (IOP)
IOP (fluid pressure inside the eye) was assessed using Goldmann applanation tonometry or Tonopen and measured in millimeters of mercury (mmHg). A higher IOP can be a greater risk factor for developing glaucoma or glaucoma progression (leading to optic nerve damage). Both eyes contributed to the analysis.
Percentage of Subjects With Increase in Slit-Lamp Parameter From Baseline to Any Visit
Ocular signs (cornea, lens, and iris/anterior chamber) were assessed by slit-lamp biomicroscopy. An increase indicates worsening. Only one eye contributed to the analysis.
Percentage of Subjects With Increase in Dilated Fundus Parameter From Baseline to Any Visit
The dilated fundus examination was performed to evaluate the health of the vitreous, retina, macula, choroid, and optic nerve. An increase indicates worsening. Only one eye contributed to the analysis.
Secondary Outcome Measures
Percentage of Subjects With More Than 20 Units Improvement in Global Ocular Discomfort Score From Baseline at Day 71
Discomfort frequency and severity (each graded on a separate 100-units scale) were assessed daily using a VAS displayed on a handheld ePRO. Frequency score was in response to the question 'how often your eyes felt uncomfortable during the past 24 hours' ranging from 'Rarely' to 'All the time.' Severity score was in response to the question 'how uncomfortable your eyes felt during the past 24 hours' ranging from 'Very mildly uncomfortable' to 'Very severely uncomfortable.' The Global Ocular Discomfort Score, ranging from 0 to 100, was calculated for any given day, as the square root of the product of the discomfort frequency score multiplied by the discomfort severity score. Improvement results in a reduction of the discomfort frequency or severity, or both, translating into a reduction of the resulting Global Ocular Discomfort score as compared to baseline.
Percentage of Subjects With LME636 Serum Concentrations Below the Lower Limit of Quantification (LLOQ)
Serum concentrations at each collection time point were quantitated, where possible, using a validated immunoassay method. LLOQ is defined as 0.25 ng/mL.
Percentage of Subjects With Anti-LME636 Antibodies by Visit
Samples were collected and assessed for anti-LME636 antibodies.
Full Information
NCT ID
NCT02365519
First Posted
February 13, 2015
Last Updated
May 31, 2018
Sponsor
Alcon, a Novartis Company
Collaborators
Novartis Institutes for BioMedical Research
1. Study Identification
Unique Protocol Identification Number
NCT02365519
Brief Title
LME636 in the Relief of Persistent Ocular Discomfort in Subjects With Severe Dry Eye Disease
Official Title
A Randomized, Double-masked, Vehicle-controlled Study of LME636 in the Relief of Persistent Ocular Discomfort in Subjects With Severe Dry Eye Disease
Study Type
Interventional
2. Study Status
Record Verification Date
October 2017
Overall Recruitment Status
Completed
Study Start Date
March 9, 2015 (Actual)
Primary Completion Date
October 16, 2015 (Actual)
Study Completion Date
October 16, 2015 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Alcon, a Novartis Company
Collaborators
Novartis Institutes for BioMedical Research
4. Oversight
Studies a U.S. FDA-regulated Drug Product
Yes
Studies a U.S. FDA-regulated Device Product
No
Data Monitoring Committee
No
5. Study Description
Brief Summary
The purpose of this study is to evaluate the efficacy of LME636 compared to vehicle in the reduction of ocular symptoms and to evaluate the safety and tolerability of LME636, when administered topically for up to 42 days, in subjects with severe dry eye disease.
Detailed Description
This study is organized into 2 phases. Following a 2-week identification phase, eligible subjects with severe dry eye disease (DED) will be randomized into the treatment phase and will be dispensed study treatment for 10 weeks.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Dry Eye
Keywords
LME636, dry eye disease, efficacy, ocular discomfort
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Parallel Assignment
Masking
ParticipantInvestigator
Allocation
Randomized
Enrollment
514 (Actual)
8. Arms, Groups, and Interventions
Arm Title
LME636
Arm Type
Experimental
Arm Description
LME636 ophthalmic solution, 1 drop (approx. 40 µL; 2.4 mg) administered topically in each eye 3 times a day (TID) for 6 weeks
Arm Title
Vehicle
Arm Type
Placebo Comparator
Arm Description
LME636 Vehicle, 1 drop administered topically in each eye TID for 6 weeks
Intervention Type
Biological
Intervention Name(s)
LME636 ophthalmic solution
Intervention Type
Biological
Intervention Name(s)
LME636 Vehicle
Intervention Description
Inactive ingredients used as a placebo comparator
Primary Outcome Measure Information:
Title
Mean Change From Baseline in Global Ocular Discomfort Score at Day 71
Description
Discomfort frequency and severity (each graded on a separate 100-units scale) were assessed daily using a visual analog scale (VAS) displayed on a handheld digital Pad (electronic patient-reported outcome (ePRO)). Frequency score was in response to the question 'how often your eyes felt uncomfortable during the past 24 hours' ranging from 'Rarely' to 'All the time.' Severity score was in response to the question 'how uncomfortable your eyes felt during the past 24 hours' ranging from 'Very mildly uncomfortable' to 'Very severely uncomfortable.' The Global Ocular Discomfort Score, ranging from 0 to 100, was calculated for any given day, as the square root of the product of the discomfort frequency score multiplied by the discomfort severity score. Improvement results in a reduction of the discomfort frequency or severity, or both, translating into a reduction of the resulting Global Ocular Discomfort score as compared to baseline. A negative change from baseline indicates improvement.
Time Frame
Baseline (Day 43), Day 71
Title
Best Corrected Visual Acuity (BCVA)
Description
Visual Acuity (VA) with the subject's best spectacles or other visual corrective devices was measured using an ETDRS visual acuity chart at 3 meters (10 feet) and reported in letters read correctly. An increase (gain) in letters read indicates improvement. Both eyes contributed to the analysis.
Time Frame
Baseline (Day 43), Day 57, Day 71, Day 85
Title
Intraocular Pressure (IOP)
Description
IOP (fluid pressure inside the eye) was assessed using Goldmann applanation tonometry or Tonopen and measured in millimeters of mercury (mmHg). A higher IOP can be a greater risk factor for developing glaucoma or glaucoma progression (leading to optic nerve damage). Both eyes contributed to the analysis.
Time Frame
Baseline (Day 43), Day 57, Day 71, Day 85
Title
Percentage of Subjects With Increase in Slit-Lamp Parameter From Baseline to Any Visit
Description
Ocular signs (cornea, lens, and iris/anterior chamber) were assessed by slit-lamp biomicroscopy. An increase indicates worsening. Only one eye contributed to the analysis.
Time Frame
Baseline (Day 43), Day 57, Day 71, Day 85
Title
Percentage of Subjects With Increase in Dilated Fundus Parameter From Baseline to Any Visit
Description
The dilated fundus examination was performed to evaluate the health of the vitreous, retina, macula, choroid, and optic nerve. An increase indicates worsening. Only one eye contributed to the analysis.
Time Frame
Baseline (Day 43), Day 57, Day 71, Day 85
Secondary Outcome Measure Information:
Title
Percentage of Subjects With More Than 20 Units Improvement in Global Ocular Discomfort Score From Baseline at Day 71
Description
Discomfort frequency and severity (each graded on a separate 100-units scale) were assessed daily using a VAS displayed on a handheld ePRO. Frequency score was in response to the question 'how often your eyes felt uncomfortable during the past 24 hours' ranging from 'Rarely' to 'All the time.' Severity score was in response to the question 'how uncomfortable your eyes felt during the past 24 hours' ranging from 'Very mildly uncomfortable' to 'Very severely uncomfortable.' The Global Ocular Discomfort Score, ranging from 0 to 100, was calculated for any given day, as the square root of the product of the discomfort frequency score multiplied by the discomfort severity score. Improvement results in a reduction of the discomfort frequency or severity, or both, translating into a reduction of the resulting Global Ocular Discomfort score as compared to baseline.
Time Frame
Baseline (Day 43), Day 71
Title
Percentage of Subjects With LME636 Serum Concentrations Below the Lower Limit of Quantification (LLOQ)
Description
Serum concentrations at each collection time point were quantitated, where possible, using a validated immunoassay method. LLOQ is defined as 0.25 ng/mL.
Time Frame
Day 15, Day 29, Day 43, Day 57, Day 71, Day 85
Title
Percentage of Subjects With Anti-LME636 Antibodies by Visit
Description
Samples were collected and assessed for anti-LME636 antibodies.
Time Frame
Day 15, Day 29, Day 43, Day 57, Day 71, Day 85
10. Eligibility
Sex
All
Minimum Age & Unit of Time
18 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Must sign written informed consent.
Physician diagnosis of DED of at least 6 months prior to Visit 1.
Must use artificial tears, gels, lubricants or re-wetting drops on a regular basis.
Respond as "often" or "constantly" to the question "How often do your eyes feel uncomfortable?".
Best Corrected Visual Acuity (BCVA) of 55 or greater in each eye as measured by ETDRS at Visit 1.
Other protocol-specified inclusion criteria may apply.
Exclusion Criteria:
Presence of any acute infection or non-infectious ocular condition in either eye within 1 month of Visit 1.
Contact lens wearers, defined as individuals who cannot be without their contact lenses for the entire duration of the study.
Any chronic ocular degenerative condition that in the opinion of the Investigator could possibly advance during the time course of the study.
Use of biologics treatments, such as systemic biologic anti-cytokines, including anti-TNFα drugs, or immunosuppressive therapy for the treatment of severe systemic autoimmune disorders.
Diseases or conditions affecting the ocular surface that are associated with clinically significant scarring and or destruction of conjunctiva and/or cornea.
Unwilling to abstain from topical ocular non-prescription medications during the course of the study, including concomitant use of artificial tears, gels, lubricants, re-wetting drops, allergy drops, etc. after Visit 2.
Use of nasal, inhaled, systemic (including injections), or topical corticosteroids within 30 days of Visit 1.
Women of child-bearing potential unwilling to use effective contraception methods as defined in the protocol.
Other protocol-specified exclusion criteria may apply.
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Senior Clinical Manager, GCRA
Organizational Affiliation
Alcon, A Novartis Division
Official's Role
Study Director
12. IPD Sharing Statement
Learn more about this trial
LME636 in the Relief of Persistent Ocular Discomfort in Subjects With Severe Dry Eye Disease
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