Pembrolizumab Plus Epacadostat vs Pembrolizumab Plus Placebo in Metastatic Non-Small Cell Lung Cancer (KEYNOTE-654-05/ECHO-305-05)
Lung Cancer

About this trial
This is an interventional treatment trial for Lung Cancer focused on measuring non-small cell lung cancer, programmed cell death 1 (PD-1) inhibitor, indoleamine 2, 3-dioxygenase 1 (IDO1) inhibitor
Eligibility Criteria
Inclusion Criteria:
- Histologically or cytologically confirmed diagnosis of stage IV NSCLC without epidermal growth factor receptor (EGFR)-sensitizing mutation, ROS1 and/or anaplastic lymphoma kinase (ALK) translocation.
- Measurable disease based on RECIST 1.1.
- Tumor tissue that demonstrates programmed cell death ligand 1 (PD-L1) expression in ≥ 50% of tumor cells (tumor proportion score [TPS] ≥ 50%) as assessed by immunohistochemistry at a central laboratory.
- Life expectancy of at least 3 months.
- Eastern Cooperative Oncology Group (ECOG) performance status of 0 or 1.
- Adequate organ function per protocol-defined criteria.
Exclusion Criteria:
- Known untreated central nervous system metastases and/or carcinomatous meningitis.
- History of (noninfectious) pneumonitis that required systemic steroids or current pneumonitis/interstitial lung disease.
- Symptomatic ascites or pleural effusion.
- Known history of an additional malignancy, except if the participant has undergone potentially curative therapy with no evidence of that disease recurrence for 5 years since initiation of that therapy.
- Active autoimmune disease that has required systemic treatment in past 2 years.
- Has had an allogeneic tissue/solid organ transplant.
- Has a known history of human immunodeficiency virus (HIV) infection. HIV testing is not required unless mandated by the local health authority.
- Has known history of or is positive for active Hepatitis B (HBsAg reactive) or has active Hepatitis C (HCV RNA). Note: Testing must be performed to determine eligibility.
- History or presence of an abnormal electrocardiogram (ECG) that, in the Investigator's opinion, is clinically meaningful.
- Use of protocol-defined prior/concomitant therapy.
Sites / Locations
- Pacific Cancer Medical Center, Inc.
- Innovative Clinical Research Institute
- Florida Cancer Specialists (South Region)
- Florida Cancer Specialists (North Region)
- Southeastern Regional Medical Center, Inc.
- Anne Arundel Health System Research Institute
- Weinberg Cancer Institute at Franklin Square
- Maryland Oncology Hematology, P.A.
- UMass Memorial Medical Center
- Minnesota Oncology Hematology, PA
- Nebraska Cancer Specialists
- Allegheny General Hospital
- Tennessee Oncology, PLLC/The Sarah Cannon Research Institute
- Tennessee Oncology, PLLC/The Sarah Cannon Research Institute
- Texas Oncology-South Austin
- Austin Health-Austin Hospital
- St John of God Murdoch Medical Clinic
- Cross Cancer Institute
- Moncton Hospital - Horizon Health Network
- William Osler Health System
- Cancer Centre of Southeastern Ontario at Kingston General Hospital
- Sault Area Hospital
- Rigshospitalet
- Regionshospitalet Herning
- Odense Universitetshospital
- SA Tartu Ulikooli Kliinikum
- Galway University Hospital
- St Vincents University Hospital
- Soroka Medical Center
- Rambam Medical Center
- Meir Medical Center
- Rabin Medical Center
- Chaim Sheba Medical Center
- IRCCS A.O.U. San Martino - IST
- Policlinico Universitario Agostino Gemelli
- National Hospital Organization Nagoya Medical Center
- National Hospital Organization Shikoku Cancer Center
- Kurume University Hospital
- Kanazawa University Hospital
- Kanagawa Cancer Center
- Sendai Kousei Hospital
- Kansai Medical University Hospital
- Kindai University Hospital
- Shizuoka Cancer Center
- National Hospital Organization Kyushu Cancer Center
- Kyushu University Hospital
- Niigata Cancer Center Hospital
- Okayama University Hospital
- National Cancer Center Hospital
- Nippon Medical School Hospital
- The Cancer Institute Hospital of JFCR
- Wakayama Medical University Hospital
- Chungbuk National University Hospital
- Seoul National University Bundang Hospital
- Gacheon University Gil Medical Center
- Hospital Tengku Ampuan Afzan
- Institut Kanser Negara - National Cancer Institute
- University Malaya Medical Centre
- Pantai Hospital Kuala Lumpur
- Sarawak General Hospital
- Swietokrzyskie Centrum Onkologii SPZOZ
- Centrum Onkologii im. Prof. Franciszka Lukaszczyka
- Centrum Onkologii. Instytut im. Marii Sklodowskiej-Curie
- Swietokrzyskie Centrum Onkologii SPZOZ
- Przychodnia Lekarska Komed
- Samodzielny Publiczny Zespol Gruzlicy i Chorob Pluc
- Wojewodzki Szpital im. Zofii z Zamoyskich Tarnowskiej w Tarnobrzegu
- Centrum Onkologii-Instytut im. Marii Sklodowskiej-Curie
- Belgorod Regional Oncology Dispensary
- Central Clinical Hospital with polyclinic
- Moscow Research Oncology Institute named after P.A. Hertsen
- SBHI Leningrad Regional Clinical Hospital
- SBHI Samara Regional Clinical Oncology Dispensary
- Republican Clinical Oncology Dispensary of Republic of Bashkortostan
- Hospital Alvaro Cunqueiro
- Hospital General de Alicante
- Hospital del Mar
- Hospital Clinico San Carlos
- Hospital Universitario 12 de Octubre
- Hospital Universitario Virgen Macarena
- Hospital Clinico de Valencia
- Oncological Institute of Southern Switzerland
- Inselspital Universitatsspital Bern
- Hopitaux Universitaires de Geneve HUG.
- Kantonsspital Winterthur
- Universitaetsspital Zuerich
- Basken Uni. Adana Dr.Turgut Noyan Uygulama ve Arastirma Merkezi
- Ankara University Medical Faculty
- Akdeniz Universitesi Tip Fakultesi
- Erciyes Universitesi Tip Fakultesi
- Necmettin Erbakan Universitesi Meram Tip Fakultesi Hastanesi
- MI Kryviy Rih Center of Dnipropetrovsk Regional Council
- Dnipropetrovsk City Multidiscipline Clinical Hosp.4 of DRC
- Grigoriev Institute for medical Radiology NAMS of Ukraine
- PP PPC Acinus Medical and Diagnostic Centre
- Kyiv City Clinical Oncological Center
- Dobryi Prognoz
- Volyn Regional Oncological Dispensary
- MI Odessa Regional Oncological Centre
- Zaporizhzhya Regional Clinical Oncology Center
- Leeds Teaching Hospital NHS Trust. St. James University Hospital
Arms of the Study
Arm 1
Arm 2
Experimental
Active Comparator
Pembrolizumab + Epacadostat
Pembrolizumab + Placebo
Participants received pembrolizumab 200 mg as an intravenous (IV) infusion, every three weeks (Q3W) starting on Day 1 of each cycle for up to 35 administrations in combination with epacadostat 100 mg orally, twice daily. Epacodostat administration was discontinued after the implementation of protocol amendment 05.
Participants received pembrolizumab 200 mg by IV infusion, Q3W starting on Day 1 of each cycle for up to 35 administrations in combination with matching placebo orally, twice daily. Placebo administration was discontinued after the implementation of protocol amendment 05.