Eltrombopag in Chronic ITP
Primary Purpose
Immune Thrombocytopenia
Status
Unknown status
Phase
Phase 4
Locations
Study Type
Interventional
Intervention
Eltrombopag
Sponsored by
About this trial
This is an interventional treatment trial for Immune Thrombocytopenia
Eligibility Criteria
Inclusion Criteria:
- Pediatric patients with chronic ITP aged 1 to 17 years.
- Platelet count is less than 30×109 per liter.
- Patients neither have had spontaneous resolution of the thrombocytopenia nor responded to corticosteroids and/or IV immunoglobulin.
Exclusion Criteria:
- Patients with clinical and/or laboratory evidence of hepatotoxicity/liver decompensation (Hepatotoxicity due to eltrombopag is defined as increased serum alanine aminotransferase ≥3 times the upper limit of normal (ULN), aspartate aminotransferase ≥3 ULN, alkaline phosphatase >1.5 ULN, total bilirubin >1.5 ULN)
- Patients with history of thrombotic/thromboembolic events.
Sites / Locations
Outcomes
Primary Outcome Measures
Measuring the platelet count response to eltrombopag in pediatric chronic ITP
Secondary Outcome Measures
Full Information
NCT ID
NCT04102033
First Posted
September 23, 2019
Last Updated
September 23, 2019
Sponsor
Assiut University
1. Study Identification
Unique Protocol Identification Number
NCT04102033
Brief Title
Eltrombopag in Chronic ITP
Official Title
Efficacy of Eltrombopag in Chronic Immune Thrombocytopenia in Pediatrics
Study Type
Interventional
2. Study Status
Record Verification Date
September 2019
Overall Recruitment Status
Unknown status
Study Start Date
November 1, 2019 (Anticipated)
Primary Completion Date
November 1, 2020 (Anticipated)
Study Completion Date
January 1, 2021 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Principal Investigator
Name of the Sponsor
Assiut University
4. Oversight
Studies a U.S. FDA-regulated Drug Product
No
Studies a U.S. FDA-regulated Device Product
No
Data Monitoring Committee
No
5. Study Description
Brief Summary
This study aims to evaluate the efficacy of eltrombopag on the platelet count in pediatric patients with chronic immune thrombocytopenia.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Immune Thrombocytopenia
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 4
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
20 (Anticipated)
8. Arms, Groups, and Interventions
Intervention Type
Drug
Intervention Name(s)
Eltrombopag
Intervention Description
Thrombopietic agent approved for its efficacy in chronic immune thrombocytopenia in pediatric patients
Primary Outcome Measure Information:
Title
Measuring the platelet count response to eltrombopag in pediatric chronic ITP
Time Frame
6 months
10. Eligibility
Sex
All
Minimum Age & Unit of Time
1 Year
Maximum Age & Unit of Time
17 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Pediatric patients with chronic ITP aged 1 to 17 years.
Platelet count is less than 30×109 per liter.
Patients neither have had spontaneous resolution of the thrombocytopenia nor responded to corticosteroids and/or IV immunoglobulin.
Exclusion Criteria:
Patients with clinical and/or laboratory evidence of hepatotoxicity/liver decompensation (Hepatotoxicity due to eltrombopag is defined as increased serum alanine aminotransferase ≥3 times the upper limit of normal (ULN), aspartate aminotransferase ≥3 ULN, alkaline phosphatase >1.5 ULN, total bilirubin >1.5 ULN)
Patients with history of thrombotic/thromboembolic events.
Central Contact Person:
First Name & Middle Initial & Last Name or Official Title & Degree
Gehad M. Abdelsalam, M.B.B.Ch
Phone
+201091294596
Email
gehad011157@med.au.edu.eg
First Name & Middle Initial & Last Name or Official Title & Degree
Mohammed M. Hamdy Ghazaly, M.D.
Phone
+201001296603
Email
mohamed.ghazali1@med.au.edu.eg
12. IPD Sharing Statement
Citations:
PubMed Identifier
20460556
Citation
Corman SL, Mohammad RA. Eltrombopag: a novel oral thrombopoietin receptor agonist. Ann Pharmacother. 2010 Jun;44(6):1072-9. doi: 10.1345/aph.1P042. Epub 2010 May 11. Erratum In: Ann Pharmacother. 2010 Jul-Aug;44(7-8):1352-3.
Results Reference
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PubMed Identifier
26688484
Citation
Bussel JB, de Miguel PG, Despotovic JM, Grainger JD, Sevilla J, Blanchette VS, Krishnamurti L, Connor P, David M, Boayue KB, Matthews DC, Lambert MP, Marcello LM, Iyengar M, Chan GW, Chagin KD, Theodore D, Bailey CK, Bakshi KK. Eltrombopag for the treatment of children with persistent and chronic immune thrombocytopenia (PETIT): a randomised, multicentre, placebo-controlled study. Lancet Haematol. 2015 Aug;2(8):e315-25. doi: 10.1016/S2352-3026(15)00114-3. Epub 2015 Jul 28. Erratum In: Lancet Haematol. 2015 Oct;2(10):e407.
Results Reference
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Eltrombopag in Chronic ITP
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