Clinical Characteristics and Mechanism Research of Inhibitors of Janus Kinase in the Idiopathic Inflammatory Myopathies
Primary Purpose
Idiopathic Inflammatory Myopathies
Status
Recruiting
Phase
Phase 2
Locations
China
Study Type
Interventional
Intervention
tofacitinib
Sponsored by
About this trial
This is an interventional treatment trial for Idiopathic Inflammatory Myopathies
Eligibility Criteria
Inclusion Criteria:
- Adults between 18 years and 75 years of age.
- Adults with active idiopathic inflammatory myopathies will be enrolled, meeting the Bohan & Peter DM/PM or American College of Rheumatology(ACR) & European allance of associations for rheumatology(EULAR)(2017) diagnostic criteria.
- Written informed consent should be obtained from each study subject.
- Concomitant immunosuppressive agents or glucocorticoids were allowed, but subjects should have been on these therapies at least 4 weeks and on a stable dose for ≥4 weeks(glucocorticoid doses are lower than <0.5mg/kg/d).
- Consent to use effective contraception during the study (women of childbearing age).
Exclusion Criteria:
Any subject meeting either of the following criteria should be excluded:
- Laboratory abnormality: Hb<8 g/dl or platelet<60*10^9/L, or combined with severe hepatic, renal and cardiac insufficiency;
- Myositis in overlap with another systemic autoimmune rheumatic disorder, cancer-associated myositis, inclusion body myositis or any other non-immune mediated myopathy.
- Biologics such as rituximab are not allowed in the 3-month before enrollment.
- Patients with malignancy within 3 years of screening.
- Patients with hypersensitivity to study drug.
- Active infections(including but not limited to hepatitis, HIV).
- Uncontrolled mental or emotional disorders.
Sites / Locations
- Department of Rheumatology and Immunology, Peking University People's HospitalRecruiting
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
tofacitinib or baricitinib
Arm Description
Tofacitinib 5mg was taken orally once or twice a day and baricitinib 2mg or 4mg was taken orally once a day for 6 months.
Outcomes
Primary Outcome Measures
Immunological Responses
Changes of follicular helper T cells (TFH) before and after tofacitinib treatment are analysed to evaluate efficacy.
Secondary Outcome Measures
Myositis Disease Activity Assessment Tool(MDAAT)
Change of MDAAT(Myositis Disease Activity Assessment Tool) is measurement of effectiveness. MDAAT ranges from 0 to 10cm. The more severe the disease activity, the higher the score. We define response as an improvement of MDAAT at least 5%.
Full Information
NCT ID
NCT05400889
First Posted
May 16, 2022
Last Updated
October 9, 2022
Sponsor
Peking University People's Hospital
1. Study Identification
Unique Protocol Identification Number
NCT05400889
Brief Title
Clinical Characteristics and Mechanism Research of Inhibitors of Janus Kinase in the Idiopathic Inflammatory Myopathies
Official Title
Real-world Experience With Inhibitors of Janus Kinase for the Treatment of Idiopathic Inflammatory Myopathies -- a Prospective Observational Study
Study Type
Interventional
2. Study Status
Record Verification Date
October 2022
Overall Recruitment Status
Recruiting
Study Start Date
June 10, 2022 (Actual)
Primary Completion Date
March 1, 2023 (Anticipated)
Study Completion Date
June 1, 2023 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Principal Investigator
Name of the Sponsor
Peking University People's Hospital
4. Oversight
Studies a U.S. FDA-regulated Drug Product
No
Studies a U.S. FDA-regulated Device Product
No
5. Study Description
Brief Summary
This study aims to explore the clinical characteristics and mechanism of inhibitors of janus kinase in the treatment of idiopathic inflammatory myopathies
Detailed Description
The investigators designed a single center, open-label, prospective study. Adults with active idiopathic inflammatory myopathies will be enrolled, meeting the Bohan & Peter Dermatomyositis/Polymyositis(DM/PM) or Rheumatology(ACR) & European allance of associations for rheumatology(EULAR)(2017) diagnostic criteria. Inhibitors of janus kinase including tofacitinib 5 mg once a day or twice a day and baricitinib 2mg once a day or 4mg once a day was administered for 6 months to explore its efficacy and safety, which could help to evaluate inhibitors of janus kinase's clinical characteristics and mechanism. Patients would be evaluated the improvement of clinical and laboratory indexes. Changes of symptoms, immune cell subsets and cytokines were monitored. Symptoms were evaluated by Visual Analogue Scale (VAS) of patient global and physician global, manual muscle testing(MMT-8), the Health Assessment Questionnaire(HAQ), Creatine kinase, Myositis Disease Activity Assessment Tool(MDAAT).
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Idiopathic Inflammatory Myopathies
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
10 (Anticipated)
8. Arms, Groups, and Interventions
Arm Title
tofacitinib or baricitinib
Arm Type
Experimental
Arm Description
Tofacitinib 5mg was taken orally once or twice a day and baricitinib 2mg or 4mg was taken orally once a day for 6 months.
Intervention Type
Drug
Intervention Name(s)
tofacitinib
Other Intervention Name(s)
Baricitinib
Intervention Description
Tofacitinib 5mg was taken orally once or twice a day and baricitinib 2mg or 4mg was taken orally once a day for 6 months.
Primary Outcome Measure Information:
Title
Immunological Responses
Description
Changes of follicular helper T cells (TFH) before and after tofacitinib treatment are analysed to evaluate efficacy.
Time Frame
week 24
Secondary Outcome Measure Information:
Title
Myositis Disease Activity Assessment Tool(MDAAT)
Description
Change of MDAAT(Myositis Disease Activity Assessment Tool) is measurement of effectiveness. MDAAT ranges from 0 to 10cm. The more severe the disease activity, the higher the score. We define response as an improvement of MDAAT at least 5%.
Time Frame
week 24
10. Eligibility
Sex
All
Minimum Age & Unit of Time
18 Years
Maximum Age & Unit of Time
75 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Adults between 18 years and 75 years of age.
Adults with active idiopathic inflammatory myopathies will be enrolled, meeting the Bohan & Peter DM/PM or American College of Rheumatology(ACR) & European allance of associations for rheumatology(EULAR)(2017) diagnostic criteria.
Written informed consent should be obtained from each study subject.
Concomitant immunosuppressive agents or glucocorticoids were allowed, but subjects should have been on these therapies at least 4 weeks and on a stable dose for ≥4 weeks(glucocorticoid doses are lower than <0.5mg/kg/d).
Consent to use effective contraception during the study (women of childbearing age).
Exclusion Criteria:
Any subject meeting either of the following criteria should be excluded:
Laboratory abnormality: Hb<8 g/dl or platelet<60*10^9/L, or combined with severe hepatic, renal and cardiac insufficiency;
Myositis in overlap with another systemic autoimmune rheumatic disorder, cancer-associated myositis, inclusion body myositis or any other non-immune mediated myopathy.
Biologics such as rituximab are not allowed in the 3-month before enrollment.
Patients with malignancy within 3 years of screening.
Patients with hypersensitivity to study drug.
Active infections(including but not limited to hepatitis, HIV).
Uncontrolled mental or emotional disorders.
Central Contact Person:
First Name & Middle Initial & Last Name or Official Title & Degree
Xiaoyan Xing
Phone
+86 18518732225
Email
1119745376@qq.com
First Name & Middle Initial & Last Name or Official Title & Degree
Jing He
Phone
+86 18611707347
Email
hejing1105@126.com
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Zhanguo Li
Organizational Affiliation
Peking University Institute of Rheuamotology and Immunology
Official's Role
Principal Investigator
Facility Information:
Facility Name
Department of Rheumatology and Immunology, Peking University People's Hospital
City
Beijing
State/Province
Beijing
Country
China
Individual Site Status
Recruiting
Facility Contact:
First Name & Middle Initial & Last Name & Degree
Jing He
Phone
+8618611707347
Email
hejing1105@126.com
12. IPD Sharing Statement
Learn more about this trial
Clinical Characteristics and Mechanism Research of Inhibitors of Janus Kinase in the Idiopathic Inflammatory Myopathies
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