Outpatient Rehabilitation Intervention for Young Children With Spinal Muscular Atrophy (SMA) Treated With Genetic Based Therapy
Spinal Muscular Atrophy
About this trial
This is an interventional treatment trial for Spinal Muscular Atrophy focused on measuring young children, pediatric, rehabilitation, feasibility study, pilot study
Eligibility Criteria
Inclusion Criteria: SMA (Type I, II or III) diagnosis; Receives genetic based therapy; Aged 6 months to 3 years old; Able to participate in weekly therapy at Holland Bloorview (i.e., can attend in-person sessions); Able to bring appropriate respiratory equipment to weekly therapy sessions, if required; Substitute decision makers (SDMs) must be able to speak and read English; Child participant must be able to understand/follow directions in English, as age appropriate; SDMs must consent to participate on behalf of their child. Exclusion Criteria: Live outside of Ontario; Tracheostomy or use of daytime ventilation (excluding ventilation used during naps).
Sites / Locations
- Holland Bloorview Kids Rehabilitation HospitalRecruiting
Arms of the Study
Arm 1
Experimental
Intervention
Participants will participate in the rehabilitation intervention.