A Prospective, Interventional Study Assessing Response to Cytarabine, Daunorubicin and Etoposide (ADE) for First Relapse of Paediatric Acute Myeloid Leukemia
Primary Purpose
Acute Myeloid Leukemia, in Relapse
Status
Unknown status
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
ADE Protocol
Sponsored by
About this trial
This is an interventional treatment trial for Acute Myeloid Leukemia, in Relapse
Eligibility Criteria
Inclusion Criteria:
- Either gender with age ≤18 years at initial diagnosis
- AML(non-M3) patients at first relapse (medullary)
Exclusion Criteria:
- Primary refractory AML &secondary AML
- More than or equal to 2 relapses of AML
- Symptomatic cardiac dysfunction (CTCAE Grade 3 or 4)
- Active infection(pneumonia etc.)
- Any other organ dysfunction (CTCAE Grade 4)
- Patients not willing to consent for the study
Sites / Locations
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
ADE arm
Arm Description
ADE arm Cytarabine (100mg/m2 d1-d10 BD), Daunorubicin (50mg/m2 d1-d3) and Etoposide (100 mg/m2 d1-5) over a period of 10 days
Outcomes
Primary Outcome Measures
complete remission (CR) rate
To assess the complete remission (CR) rate with the use of ADE chemotherapy in relapsed acute myeloid leukemia (AML) after first CR
Secondary Outcome Measures
Event free survival (EFS) and overall survival(OS)
To determineevent free survival(EFS) and overall survival(OS)
toxicity of chemotherapy
To assess the toxicity of chemotherapy using CTCAE 4.0
clonal evolution
To evaluate clonal evolution using cytogenetics &RT-PCR panel
minimal residual disease (MRD)
To assess minimal residual disease (MRD) by using flow cytometry
cardiac function
To evaluate cardiac function using 2 Dimensional Echocardiography
Full Information
NCT ID
NCT03053206
First Posted
February 7, 2017
Last Updated
February 10, 2017
Sponsor
All India Institute of Medical Sciences, New Delhi
1. Study Identification
Unique Protocol Identification Number
NCT03053206
Brief Title
A Prospective, Interventional Study Assessing Response to Cytarabine, Daunorubicin and Etoposide (ADE) for First Relapse of Paediatric Acute Myeloid Leukemia
Official Title
RESPONSE TO CYTARABINE, DAUNORUBICIN AND ETOPOSIDE (ADE) AT FIRST RELASPE IN CHILDHOOD AML
Study Type
Interventional
2. Study Status
Record Verification Date
February 2017
Overall Recruitment Status
Unknown status
Study Start Date
February 15, 2017 (Anticipated)
Primary Completion Date
December 31, 2019 (Anticipated)
Study Completion Date
December 31, 2019 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Principal Investigator
Name of the Sponsor
All India Institute of Medical Sciences, New Delhi
4. Oversight
Studies a U.S. FDA-regulated Drug Product
No
Studies a U.S. FDA-regulated Device Product
No
Data Monitoring Committee
No
5. Study Description
Brief Summary
One-third to one-half of patients with AML relapse and in general relapsed AML patients have a poor prognosis. The treatment of relapsed AML consists of induction chemotherapy followed by Allogenic Stem Cell Transplant (ASCT). However, at present there is no standard salvage chemotherapy regimen for relapsed AML, as no study has shown any one regimen to be significantly superior. Anthracyclines, Fludarabine, Etoposide and cytarabineare active agents in AMLand have been used as monotherapy and in combination in refractory and relapsed AML patients. According to previous studies the present CR rate of different regimens ranges from 50-70%. A retrospective analysis (unpublished) conducted at IRCH, AIIMS on relapsed AML patients treated with ADE (Cytarabine, Daunorubicin and Etoposide) chemotherapy showed the CR rates of approximately 70%. Therefore, we have planned this study to test the efficacy and toxicity of ADE induction chemotherapy in relapsed AML patients in a prospective manner.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Acute Myeloid Leukemia, in Relapse
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
84 (Anticipated)
8. Arms, Groups, and Interventions
Arm Title
ADE arm
Arm Type
Experimental
Arm Description
ADE arm
Cytarabine (100mg/m2 d1-d10 BD), Daunorubicin (50mg/m2 d1-d3) and Etoposide (100 mg/m2 d1-5) over a period of 10 days
Intervention Type
Drug
Intervention Name(s)
ADE Protocol
Intervention Description
ADE chemotherapy
Cytarabine (100mg/m2 d1-d10 BD), Daunorubicin (50mg/m2 d1-d3) and Etoposide (100 mg/m2 d1-5) over a period of 10 days
Primary Outcome Measure Information:
Title
complete remission (CR) rate
Description
To assess the complete remission (CR) rate with the use of ADE chemotherapy in relapsed acute myeloid leukemia (AML) after first CR
Time Frame
Day 28 ± 7 of treatment or after recovery of blood counts whichever is earlier
Secondary Outcome Measure Information:
Title
Event free survival (EFS) and overall survival(OS)
Description
To determineevent free survival(EFS) and overall survival(OS)
Time Frame
2 year
Title
toxicity of chemotherapy
Description
To assess the toxicity of chemotherapy using CTCAE 4.0
Time Frame
Day 28 ± 7 of treatment
Title
clonal evolution
Description
To evaluate clonal evolution using cytogenetics &RT-PCR panel
Time Frame
Day 28 ± 7 of treatment
Title
minimal residual disease (MRD)
Description
To assess minimal residual disease (MRD) by using flow cytometry
Time Frame
Day 28 ± 7 of treatment or after recovery of blood counts whichever is earlier
Title
cardiac function
Description
To evaluate cardiac function using 2 Dimensional Echocardiography
Time Frame
Day 28 ± 7 of treatment
10. Eligibility
Sex
All
Maximum Age & Unit of Time
18 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Either gender with age ≤18 years at initial diagnosis
AML(non-M3) patients at first relapse (medullary)
Exclusion Criteria:
Primary refractory AML &secondary AML
More than or equal to 2 relapses of AML
Symptomatic cardiac dysfunction (CTCAE Grade 3 or 4)
Active infection(pneumonia etc.)
Any other organ dysfunction (CTCAE Grade 4)
Patients not willing to consent for the study
Central Contact Person:
First Name & Middle Initial & Last Name or Official Title & Degree
ARUN GARG, DM
Phone
9968588792
Email
arungarg_aiims@yahoo.com
12. IPD Sharing Statement
Plan to Share IPD
No
Learn more about this trial
A Prospective, Interventional Study Assessing Response to Cytarabine, Daunorubicin and Etoposide (ADE) for First Relapse of Paediatric Acute Myeloid Leukemia
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