A Safety and Tolerability Study of Denufosol in 2-4 Year Olds (REACH-1)
Primary Purpose
Cystic Fibrosis
Status
Completed
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
denufosol tetrasodium Inhalation Solution
0.9% w/v sodium chloride solution
Sponsored by
About this trial
This is an interventional treatment trial for Cystic Fibrosis
Eligibility Criteria
Inclusion Criteria:
- Have a confirmed diagnosis of CF
- Have oxyhemoglobin saturation ≥ 95% prior to randomization
Exclusion Criteria:
- Have acute intercurrent respiratory infection (cough, wheezing, or new
rhinorrhea or nasal congestion)
- Have any significant medical condition not related to CF
- Unable to discontinue use of hypertonic saline
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm Type
Experimental
Placebo Comparator
Arm Label
denufosol tetrasodium Inhalation Solution
Placebo
Arm Description
Outcomes
Primary Outcome Measures
Intolerability to study drug as measured by: oxyhemoglobin saturation, treatment-emergent cough, and new wheezes or crackles
Secondary Outcome Measures
Mean change from pre-dose in oxyhemoglobin saturation at defined times post-dose
Mean change from baseline in oxyhemoglobin saturation
Incidence of treatment-emergent adverse events (TEAEs), serious adverse events (SAEs) and/or withdrawals due to TEAEs
Mean change from pre-dose in pulse and respiratory rate at defined times post-dose
Mean change from baseline in pulse and respiratory rate
Incidence of new medical condition(s) or worsening of previous medical condition(s) from baseline
Full Information
NCT ID
NCT01181622
First Posted
August 12, 2010
Last Updated
December 29, 2014
Sponsor
Merck Sharp & Dohme LLC
1. Study Identification
Unique Protocol Identification Number
NCT01181622
Brief Title
A Safety and Tolerability Study of Denufosol in 2-4 Year Olds
Acronym
REACH-1
Official Title
A Phase 2, Multi-Center, Randomized, Double-Blind, Placebo-Controlled, Parallel-Group, 7-Day Safety and Tolerability Study of Denufosol Tetrasodium Inhalation Solution Administered Via PARI LC® Star in Patients 2 to 4 Years of Age With Cystic Fibrosis
Study Type
Interventional
2. Study Status
Record Verification Date
December 2014
Overall Recruitment Status
Completed
Study Start Date
August 2010 (undefined)
Primary Completion Date
October 2010 (Actual)
Study Completion Date
October 2010 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Merck Sharp & Dohme LLC
4. Oversight
Data Monitoring Committee
Yes
5. Study Description
Brief Summary
The purpose of this study is to evaluate the safety and tolerability of denufosol 60 mg TID in pediatric CF patients 2 to 4 years of age
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Cystic Fibrosis
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Parallel Assignment
Masking
ParticipantInvestigator
Allocation
Randomized
Enrollment
25 (Actual)
8. Arms, Groups, and Interventions
Arm Title
denufosol tetrasodium Inhalation Solution
Arm Type
Experimental
Arm Title
Placebo
Arm Type
Placebo Comparator
Intervention Type
Drug
Intervention Name(s)
denufosol tetrasodium Inhalation Solution
Intervention Description
60 mg by oral inhalation three times daily
Intervention Type
Drug
Intervention Name(s)
0.9% w/v sodium chloride solution
Intervention Description
0.9% w/v sodium chloride solution by oral inhalation three times daily
Primary Outcome Measure Information:
Title
Intolerability to study drug as measured by: oxyhemoglobin saturation, treatment-emergent cough, and new wheezes or crackles
Time Frame
Day 1, Day 7
Secondary Outcome Measure Information:
Title
Mean change from pre-dose in oxyhemoglobin saturation at defined times post-dose
Time Frame
Day 1, Day 7
Title
Mean change from baseline in oxyhemoglobin saturation
Time Frame
Day 7
Title
Incidence of treatment-emergent adverse events (TEAEs), serious adverse events (SAEs) and/or withdrawals due to TEAEs
Time Frame
Day 7
Title
Mean change from pre-dose in pulse and respiratory rate at defined times post-dose
Time Frame
Day 1, Day 7
Title
Mean change from baseline in pulse and respiratory rate
Time Frame
Day 7
Title
Incidence of new medical condition(s) or worsening of previous medical condition(s) from baseline
Time Frame
Day 7
10. Eligibility
Sex
All
Minimum Age & Unit of Time
2 Years
Maximum Age & Unit of Time
4 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Have a confirmed diagnosis of CF
Have oxyhemoglobin saturation ≥ 95% prior to randomization
Exclusion Criteria:
Have acute intercurrent respiratory infection (cough, wheezing, or new
rhinorrhea or nasal congestion)
Have any significant medical condition not related to CF
Unable to discontinue use of hypertonic saline
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Lynn Smiley, MD
Organizational Affiliation
Medical monitor
Official's Role
Study Director
12. IPD Sharing Statement
Learn more about this trial
A Safety and Tolerability Study of Denufosol in 2-4 Year Olds
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