A Study of Erdafitinib Versus Investigator Choice of Intravesical Chemotherapy in Participants Who Received Bacillus Calmette-Guérin (BCG) and Recurred With High Risk Non-Muscle-Invasive Bladder Cancer (NMIBC)
Urinary Bladder Neoplasms
About this trial
This is an interventional treatment trial for Urinary Bladder Neoplasms focused on measuring Non muscle invasive bladder cancer (NMIBC), Bacillus calmette- guerin (BCG) failure, BCG unresponsive
Eligibility Criteria
Inclusion Criteria:
- Histologically confirmed, recurrent, non-muscle-invasive urothelial carcinoma of the bladder. Variant pathology are allowed
- Tumor with specified fibroblast growth factor receptor (FGFR) mutations or fusions
- Bacillus Calmette- Guerin (BCG)-unresponsive after adequate BCG therapy or BCG experienced participants
- Refuses or is not eligible for cystectomy (Cohort 1 and Cohort 2 only)
- Eastern Cooperative Oncology Group (ECOG) performance status Grade 0-1
- Must sign an informed consent form (ICF) (or their legally acceptable representative must sign) indicating that he or she understands the purpose of, and procedures required for, the study and is willing to participate in the study
- A woman of childbearing potential must have a negative pregnancy test (beta-hCG [beta-human chorionic gonadotropin]) (urine or serum) within 7 days before randomization (Cohort 1) or the first dose of study drug (Cohort 2 and Cohort 3)
- Adequate bone marrow, liver, and renal function as specified in the protocol
Exclusion Criteria:
- Histologically confirmed, muscle-invasive (T2 or higher stage) urothelial carcinoma of the bladder
- Histopathology demonstrating any small cell component, pure adenocarcinoma, pure squamous cell carcinoma, or pure squamous CIS of the bladder
- Prior treatment with an FGFR inhibitor
- Active malignancies other than the disease being treated under study. The only allowed exceptions are: (a) skin cancer treated within the last 24 months that is considered completely cured (b) adequately treated lobular carcinoma in situ (LCIS) and ductal CIS (c) history of localized breast cancer and receiving antihormonal agents, or history of localized prostate cancer (N0M0) and receiving androgen deprivation therapy
- Current central serous retinopathy or retinal pigment epithelial detachment of any grade
Sites / Locations
- Urological Associates of Southern Arizona, P.C.
- USC Institute of Urology
- The Urology Center of Colorado
- Urological Research Network
- Emory University - Winship Cancer Institute
- Northwestern University
- Simmons Cancer Institute
- University of Kansas
- Albany Medical College
- Montefiore Medical Center
- NYU Langone Health
- Great Lakes Physician PC d/b/a Western New York Urology Associates
- Levine Cancer Institute
- The Urology Group
- The Ohio State University- James Cancer Hospital
- Oregon Health & Science University
- MidLantic Urology
- University of Pittsburgh Medical Center - Cancer Centers
- Urology Associates
- UT Southwestern Medical Center
- University of Washington
- Medical College of Wisconsin-Froedtert Hospital
- Sociedade Beneficente de Senhoras - Hospital Sírio Libanês
- Hospital Britanico de Buenos Aires
- CEMIC Saavedra
- Hospital Italiano de Buenos Aires
- Cemaic - Centro Privado de Especialidades Medicas Ambulatorias e Investigacion Clinica
- Centro Urologico Profesor Bengio
- Hospital Privado de Cordoba
- Flinders Medical Centre
- St. Vincent's Hospital Sydney
- Macquarie University
- Peter MacCallum Cancer Centre
- AZ Maria Middelares
- UZ Leuven
- CHU Sart-Tilman
- Algemeen Ziekenhuis Delta
- Liga Paranaense de Combate ao Cancer
- Oncocentro Ceará
- Associacao de Combate ao Cancer em Goias - Hospital de Cancer Araujo Jorge
- Liga Norte Riograndense Contra O Cancer
- Irmandade Santa Casa de Misericordia de Porto Alegre
- Hospital Nossa Senhora da Conceicao S.A
- Instituto de Medicina Integral Professor Fernando Figueira
- Hospital das Clínicas da Faculdade de Medicina de RPUSP - HCRP
- Oncoclínicas Rio de Janeiro S.A.
- Instituto de Educacao, Pesquisa e Gestao em Saude Instituto Americas (COI)
- CEPHO - Centro de Estudos e Pesquisa de Hematologia e Oncologia
- Fundacao Faculdade de Medicina - Instituto do Cancer do Estado de Sao Paulo
- Instituto de Assistencia Medica ao Servidor Publico Estadual - IAMSPE
- Sociedade Beneficente de Senhoras - Hospital Sírio Libanês
- Nanjing Drum Tower Hospital
- Fudan University Shanghai Cancer Center
- Renji Hospital, Shanghai Jiaotong University School of Medicine
- Tongji Hospital, Tongji Medical College of Huazhong University of Science and Technology
- Fakultni nemocnice u sv. Anny v Brne
- Krajská nemocnice Liberec
- Vseobecna fakultni nemocnice v Praze
- Fakultni nemocnice v Motole
- Hopital Pellegrin CHU Bordeaux
- CHU Gabriel-Montpied
- Hopital Huriez
- Hôpital Edouard Herriot
- Institut Paoli Calmettes
- Hôpital Universitaire Pitié-Salpêtrière
- Groupe Hospitalier Diaconesses Croix Saint Simon
- Hopital Bichat Claude Bernard
- CHU De Poitiers
- Chu Rennes - Hopital Pontchaillou
- Hopital Charles Nicolle
- CHP Saint Gregoire
- Institut Universitaire du Cancer Toulouse Oncopole
- Centre Hospitalier Universitaire de Nancy - Hôpital Central
- Gustave Roussy
- Urologicum Duisburg
- Klinikum Herne - Urologie
- Universitätsklinikum Schleswig Holstein Campus Lübeck
- Klinikum rechts der Isar - III. Med. Klinik und Poliklinik
- Universitaetsklinikum Muenster
- Praxisklinik Urologie Rhein/Ruhr - Germany
- MVZ Urologie 24 gGmbH
- Studienpraxis Urologie Drs. Feyerabend
- CUROS - Uberörtliche urologische Gemeinschaftspraxis
- Health Care Global Enterprises pvt Ltd
- Rajiv Gandhi Cancer Institute & Research Centre
- King George's Medical University
- Meenakshi Mission Hospital and Research Center
- Muljibhai Patel Urological Hospital
- CIMET's Inamdar Multispeciality Hospital
- Ente Ecclesiastico Ospedale Generale Regionale F. Miulli
- Ospedale Regionale Umberto Parini
- Fondazione Istituto G. Giglio
- Ospedale Civile di Guastalla
- Azienda Ospedaliera ''Vito Fazzi''
- UOC Oncologia Ospedale Provinciale di Macerata
- Fondazione IRCCS Istituto Nazionale dei Tumori
- IRCCS Ospedale San Raffaele
- Fondazione G. Pascale - Istituto Nazionale Tumori IRCCS
- Azienda Ospedaliera Sant Andrea
- Azienda Ospedaliera Universitaria Integrata Verona
- Juntendo University Hospital
- Tokyo Medical and Dental University Hospital
- Asahi General Hospital
- Hakodate Goryokaku Hospital
- Saitama Medical University International Medical Center
- Hitachi General Hospital
- St.Marianna University Hospital
- Nagoya University Hospital
- JOHAS Osaka Rosai Hospital
- Gunma Prefectural Cancer Center
- Osaka Medical and Pharmaceutical University Hospital
- Toranomon Hospital
- The Cancer Institute Hospital of JFCR
- Fujita Health University Hospital
- University of Tsukuba Hospital
- Yokohama City University Medical Center
- Pusan National University Hospital
- Chungbuk National University Hospital
- Kyungpook National University Chilgok Hospital
- National Cancer Center
- Chonnam National University Hwasun Hospital
- Korea University Anam Hospital
- Seoul National University Hospital
- Kangbuk Samsung Hospital
- Severance Hospital, Yonsei University Health System
- Samsung Medical Center
- Uniwersyteckie Centrum Kliniczne
- Pratia MCM Krakow
- Uniwersytecki Szpital Kliniczny im. Fryderyka Chopina w Rzeszowie
- Samodzielny Publiczny Szpital Kliniczny nr 2 PUM
- City Clinic Sp. z o.o.
- Medical Concierge Centrum Medyczne
- Uniwersytecki Szpital Kliniczny
- Fundacion Puigvert
- Hosp. Clinic I Provincial de Barcelona
- Hosp. Univ. Ramon Y Cajal
- Hosp. Univ. 12 de Octubre
- Hosp. Univ. La Paz
- Corporacio Sanitari Parc Tauli
- Hosp. Univ. Marques de Valdecilla
- Instituto Valenciano de Oncologia
- Kaohsiung Medical University Chung-Ho Memorial Hospital
- China Medical University Hospital
- Taichung Veterans General Hospital
- National Taiwan University Hospital
- Taipei Veterans General Hospital
- Chang Gung Memorial Hospital- Linkou
- The Christie NHS Foundation Trust - Christie Hospital
- Universirty of Sheffield Teaching Hospitals NHS Trust
- Lister Hospital
Arms of the Study
Arm 1
Arm 2
Arm 3
Arm 4
Experimental
Active Comparator
Experimental
Experimental
Cohort 1: Erdafitinib
Cohort 1: Investigators Choice
Cohort 2
Cohort 3
Participants with high-risk non-muscle-invasive bladder cancer (NMIBC) presenting as papillary tumor only (carcinoma in situ [CIS], absent), with disease recurrence after bacillus Calmette- Guerin (BCG) therapy will receive treatment with erdafitinib.
Participants with high-risk NMIBC presenting as papillary tumor only (CIS, absent), with disease recurrence after BCG therapy will receive the investigator's choice of either intravesical gemcitabine or intravesical mitomycin C (MMC) or hyperthermic MMC. Participants who are randomized to gemcitabine or MMC or hyperthermic MMC in Cohort 1 and demonstrate a recurrence via investigator disease assessment will have the opportunity to cross over to treatment with erdafitinib.
Participants with high-risk, BCG- unresponsive NMIBC presenting as CIS with or without concurrent papillary tumor will receive treatment with erdafitinib.
Marker lesion study in intermediate-risk NMIBC presenting as papillary disease only. All enrolled participants will receive treatment with erdafitinib.