Bevacizumab With Pelvic Radiotherapy And Primary Chemotherapy in Patients With Poor-Risk Rectal Cancer (BRANCH)
Primary Purpose
Rectal Cancer
Status
Completed
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
Radiation therapy
Oxaliplatin
Raltitrexed
levofolinic acid
5-fluorouracil
Bevacizumab
Sponsored by
About this trial
This is an interventional treatment trial for Rectal Cancer focused on measuring locally advanced, high risk, preoperative therapy
Eligibility Criteria
Inclusion Criteria:
- Patients with histologically or cytologically confirmed diagnosis of locally advanced rectal cancer (LARC) at high risk of recurrence (T4, N+, T3N0 with tumor located in the lower third of the rectum and/or circumferential resection margin (CRM) £5 mm), or LARC with resectable organ metastasis (M1).
- Age 18 years or older
- Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2
- Life expectancy of at least 12 weeks
- Measurable and/or evaluable (resectable organ metastasis)lesions according to RECIST criteria
- Neutrophils > 1500 and Platelets > 100,000 /L
- Total bilirubin < or = 1.5 time the upper-normal limits (UNL) of the Institutional normal values and ASAT (SGOT) and/or ALAT (SGPT) < or = 2.5 x UNL, or < or = 5 x UNL in case of liver metastases, alkaline phosphatase < or = 2.5 x UNL, or < or = 5 x UNL in case of liver metastases.
- Creatinine clearance > 50 mL/min or serum creatinine < or = 1.5 x UNL
- Urine dipstick of proteinuria < 2+. Patients discovered to have > or = 2+ proteinuria on dipstick urinalysis at baseline, should undergo a 24-hour urine collection and must demonstrate < or = 1 g of protein/24 hr.
- Written informed consent.
- Patients must be accessible for treatment and follow up. Patients registered on this trial must be treated and followed at the participating Center
Exclusion Criteria:
- Prior radiotherapy or chemotherapy for rectal cancer.
- Untreated brain metastases or spinal cord compression or primary brain tumours
- History or evidence upon physical examination of CNS disease unless adequately treated (e.g., seizure not controlled with standard medical therapy or history of stroke).
- History of inflammatory bowel disease and/or acute/subacute bowel occlusion
- Serious, non-healing wound, ulcer, or bone fracture
- Evidence of bleeding diathesis or coagulopathy.
- Uncontrolled hypertension
- Clinically significant (i.e. active) cardiovascular disease, for example cerebrovascular accidents (≤ 6 months), myocardial infarction (≤ 6 months), unstable angina, New York Heart Association (NYHA) grade II or greater congestive heart failure, serious cardiac arrhythmia requiring medication
- Current or recent (within 10 days prior to study treatment start) ongoing treatment with anticoagulants for therapeutic purposes.
- Chronic, daily treatment with high-dose aspirin (>325 mg/day) or other medications known to predispose to gastrointestinal ulceration.
- Treatment with any investigational drug within 30 days prior to enrolment.
- Patients with known allergy to Chinese hamster ovary cell proteins, or any of the components of the study medications
- Other co-existing malignancies or malignancies diagnosed within the last 5 years with the exception of basal and squamous cell carcinoma or cervical cancer in situ
- Major surgical procedure, open biopsy, or significant traumatic injury within 28 days prior to study treatment start, or anticipation of the need for major surgical procedure during the course of the study.
- Pregnant or lactating women. Women of childbearing potential with either a positive or no pregnancy test at baseline. Postmenopausal women must have been amenorrheic for at least 12 months to be considered of non-childbearing potential. Sexually active males and females (of childbearing potential) unwilling to practice contraception during the study.
Sites / Locations
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
preoperative chemoradiotherapy
Arm Description
Preoperative radiation therapy and combination chemotherapy plus bevacizumab
Outcomes
Primary Outcome Measures
Percentage of Patients With Complete Tumor Regression Rate (TRG1)
Complete tumor regression rate (TRG1) was the ratio of patients with TRG1, graded at surgical resection, and total patients included in the study, expressed in percentage.
Tumor regression grade (TRG) was misured according to the Mandard Scale. Briefly,TRG1 was a complete tumor regression (regardless of the presence of acellular mucine lakes), and TRG2 was a nearly complete tumor regression with extensive fibrosis; TRG3 presented with clear evidence of residual cancer cells but with predominant fibrosis;TRG4 was a residual of cancer cells outgrowing fibrosis; TRG5 was the absence of regressive changes.
Secondary Outcome Measures
Number of Participants With Adverse Events
Number of Participants with Adverse Events as a Measure of Safety and Tolerability
Number of Patients With Sphincter Preservation
Sphincter preservation in patients with tumor < 5 cm from anal verge in 8 weeks after chemoradiation therapy
Progression Free Survival (PFS)
PFS was calculated from the date of the initial treatment until tumor progression or relapse, death for any cause or last follow up.
Progression was defined using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.
Overall Survival (OS)
OS was calculated from the date of initial treatment to the date of death for any cause or last follow up.
Clinical Response Rate
Clinical response was assessed before surgery with the same imaging modalities that were used for the inclusion in the study.
Clinical response rate was the ratio between complete and partial response, evaluated by RECIST CRITERIA, and total of patients evaluated, expressed in percentage of patients.
Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions and assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), >=30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR.
Patients With Metastatic Lymphnodes at Pathology Exam After Surgery
Number of patients with metastatic lymphnodes at pathology exam after surgery.
Full Information
NCT ID
NCT01481545
First Posted
November 11, 2011
Last Updated
January 13, 2021
Sponsor
National Cancer Institute, Naples
1. Study Identification
Unique Protocol Identification Number
NCT01481545
Brief Title
Bevacizumab With Pelvic Radiotherapy And Primary Chemotherapy in Patients With Poor-Risk Rectal Cancer
Acronym
BRANCH
Official Title
Bevacizumab With Pelvic Radiotherapy And Primary Chemotherapy in Patients With Poor-Risk Rectal Cancer: the BRANCH Trial
Study Type
Interventional
2. Study Status
Record Verification Date
September 2020
Overall Recruitment Status
Completed
Study Start Date
December 2006 (Actual)
Primary Completion Date
July 2011 (Actual)
Study Completion Date
December 2016 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
National Cancer Institute, Naples
4. Oversight
Data Monitoring Committee
No
5. Study Description
Brief Summary
The purpose of this study is to evaluate the use of chemotherapy, radiation therapy and bevacizumab before surgery in patients with locally advanced rectal cancer (LARC).
Detailed Description
To determine the pathological complete response (pCR-TRG1) rate in patients treated with 2 different schedule of bevacizumab plus primary chemotherapy and radiotherapy of the pelvic region when optimal surgery is applied.
Bevacizumab will be given by intravenous infusion at the dose of 5 mg/kg concurrent with chemotherapy and radiotherapy every 2 weeks for 4 cycles from -14 days to start chemo-radiotherapy (classical schedule) or 4 days before the concurrent administration of chemotherapy and radiation therapy for 2 cycles if the number of TRG1 was not reached in the first stage with the classical schedule Simon's methods will be used to calculate sample size.Setting a and b errors as 0.05 and 0.20, respectively, and defining as minimum activity of interest (p0) a TRG1 rate=30%. In order to demonstrate a TRG1 rate ≥50% (p1), at least 6 TRG1 on the first 15 patients, and at least 19 TRG1 on a total of 46 patients should be reported in the first and second stage, respectively.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Rectal Cancer
Keywords
locally advanced, high risk, preoperative therapy
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
62 (Actual)
8. Arms, Groups, and Interventions
Arm Title
preoperative chemoradiotherapy
Arm Type
Experimental
Arm Description
Preoperative radiation therapy and combination chemotherapy plus bevacizumab
Intervention Type
Radiation
Intervention Name(s)
Radiation therapy
Intervention Description
Radiation therapy will be administered at the total dose of 45 Gy, given with five weekly fractions over a period of 5 weeks. The daily fraction dose will be 1.8 Gy
Intervention Type
Drug
Intervention Name(s)
Oxaliplatin
Intervention Description
100 mg/m2 on day 1 every 2 weeks for 3 cycles (for patients with resectable organ metastases (M1), an additional 2 cycles of chemotherapy will be given after radiation therapy)
Intervention Type
Drug
Intervention Name(s)
Raltitrexed
Intervention Description
2.5 mg/m2 on day 1 every 2 weeks for 3 cycles (for patients with resectable organ metastases (M1) , an additional 2 cycles of chemotherapy will be given after radiation therapy)
Intervention Type
Drug
Intervention Name(s)
levofolinic acid
Intervention Description
250 mg/m2 on day 2 every 2 weeks for 3 cycles (for patients with resectable organ metastases (M1), an additional 2 cycles of chemotherapy will be given after radiation therapy)
Intervention Type
Drug
Intervention Name(s)
5-fluorouracil
Intervention Description
800 mg/m2 on day 2 every 2 weeks for 3 cycles (for patients with resectable organ metastases (M1), an additional 2 cycles of chemotherapy will be given after radiation therapy)
Intervention Type
Drug
Intervention Name(s)
Bevacizumab
Intervention Description
will be given by intravenous infusion at the dose of 5 mg/kg concurrent with chemotherapy and radiotherapy every 2 weeks for 4 cycles from -14 days to start chemo-radiotherapy (classical schedule) or 4 days before the concurrent administration of chemotherapy and radiation therapy for 2 cycles if the number of TRG1 was not reached in the first stage (statistical design) with the classical schedule (for patients with resectable organ metastases (M1), one additional administration of bevacizumab will be given after radiation therapy)
Primary Outcome Measure Information:
Title
Percentage of Patients With Complete Tumor Regression Rate (TRG1)
Description
Complete tumor regression rate (TRG1) was the ratio of patients with TRG1, graded at surgical resection, and total patients included in the study, expressed in percentage.
Tumor regression grade (TRG) was misured according to the Mandard Scale. Briefly,TRG1 was a complete tumor regression (regardless of the presence of acellular mucine lakes), and TRG2 was a nearly complete tumor regression with extensive fibrosis; TRG3 presented with clear evidence of residual cancer cells but with predominant fibrosis;TRG4 was a residual of cancer cells outgrowing fibrosis; TRG5 was the absence of regressive changes.
Time Frame
In 8 weeks after completion of chemoradiotherapy
Secondary Outcome Measure Information:
Title
Number of Participants With Adverse Events
Description
Number of Participants with Adverse Events as a Measure of Safety and Tolerability
Time Frame
Up to 8 weeks after surgery
Title
Number of Patients With Sphincter Preservation
Description
Sphincter preservation in patients with tumor < 5 cm from anal verge in 8 weeks after chemoradiation therapy
Time Frame
In 8 weeks after chemoradiation therapy
Title
Progression Free Survival (PFS)
Description
PFS was calculated from the date of the initial treatment until tumor progression or relapse, death for any cause or last follow up.
Progression was defined using Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0), as a 20% increase in the sum of the longest diameter of target lesions, or a measurable increase in a non-target lesion, or the appearance of new lesions.
Time Frame
10 years
Title
Overall Survival (OS)
Description
OS was calculated from the date of initial treatment to the date of death for any cause or last follow up.
Time Frame
10 years
Title
Clinical Response Rate
Description
Clinical response was assessed before surgery with the same imaging modalities that were used for the inclusion in the study.
Clinical response rate was the ratio between complete and partial response, evaluated by RECIST CRITERIA, and total of patients evaluated, expressed in percentage of patients.
Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions and assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), >=30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR.
Time Frame
7 weeks after chemoradiation therapy up to 11 weeks
Title
Patients With Metastatic Lymphnodes at Pathology Exam After Surgery
Description
Number of patients with metastatic lymphnodes at pathology exam after surgery.
Time Frame
In 8 weeks after chemoradiation therapy completion
10. Eligibility
Sex
All
Minimum Age & Unit of Time
18 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Patients with histologically or cytologically confirmed diagnosis of locally advanced rectal cancer (LARC) at high risk of recurrence (T4, N+, T3N0 with tumor located in the lower third of the rectum and/or circumferential resection margin (CRM) £5 mm), or LARC with resectable organ metastasis (M1).
Age 18 years or older
Eastern Cooperative Oncology Group (ECOG) Performance Status 0-2
Life expectancy of at least 12 weeks
Measurable and/or evaluable (resectable organ metastasis)lesions according to RECIST criteria
Neutrophils > 1500 and Platelets > 100,000 /L
Total bilirubin < or = 1.5 time the upper-normal limits (UNL) of the Institutional normal values and ASAT (SGOT) and/or ALAT (SGPT) < or = 2.5 x UNL, or < or = 5 x UNL in case of liver metastases, alkaline phosphatase < or = 2.5 x UNL, or < or = 5 x UNL in case of liver metastases.
Creatinine clearance > 50 mL/min or serum creatinine < or = 1.5 x UNL
Urine dipstick of proteinuria < 2+. Patients discovered to have > or = 2+ proteinuria on dipstick urinalysis at baseline, should undergo a 24-hour urine collection and must demonstrate < or = 1 g of protein/24 hr.
Written informed consent.
Patients must be accessible for treatment and follow up. Patients registered on this trial must be treated and followed at the participating Center
Exclusion Criteria:
Prior radiotherapy or chemotherapy for rectal cancer.
Untreated brain metastases or spinal cord compression or primary brain tumours
History or evidence upon physical examination of CNS disease unless adequately treated (e.g., seizure not controlled with standard medical therapy or history of stroke).
History of inflammatory bowel disease and/or acute/subacute bowel occlusion
Serious, non-healing wound, ulcer, or bone fracture
Evidence of bleeding diathesis or coagulopathy.
Uncontrolled hypertension
Clinically significant (i.e. active) cardiovascular disease, for example cerebrovascular accidents (≤ 6 months), myocardial infarction (≤ 6 months), unstable angina, New York Heart Association (NYHA) grade II or greater congestive heart failure, serious cardiac arrhythmia requiring medication
Current or recent (within 10 days prior to study treatment start) ongoing treatment with anticoagulants for therapeutic purposes.
Chronic, daily treatment with high-dose aspirin (>325 mg/day) or other medications known to predispose to gastrointestinal ulceration.
Treatment with any investigational drug within 30 days prior to enrolment.
Patients with known allergy to Chinese hamster ovary cell proteins, or any of the components of the study medications
Other co-existing malignancies or malignancies diagnosed within the last 5 years with the exception of basal and squamous cell carcinoma or cervical cancer in situ
Major surgical procedure, open biopsy, or significant traumatic injury within 28 days prior to study treatment start, or anticipation of the need for major surgical procedure during the course of the study.
Pregnant or lactating women. Women of childbearing potential with either a positive or no pregnancy test at baseline. Postmenopausal women must have been amenorrheic for at least 12 months to be considered of non-childbearing potential. Sexually active males and females (of childbearing potential) unwilling to practice contraception during the study.
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Antonio Avallone, M.D.
Organizational Affiliation
National Cancer Institute, Naples
Official's Role
Principal Investigator
12. IPD Sharing Statement
Learn more about this trial
Bevacizumab With Pelvic Radiotherapy And Primary Chemotherapy in Patients With Poor-Risk Rectal Cancer
We'll reach out to this number within 24 hrs