Determining the Maximum Tolerated Dose of Low Dose Interferon-alpha in Conjunction With Nilotinib in Pretreated Philadelphia Chromosome Positive (Ph+) Chronic Myeloid Leukemia Patients in Chronic Phase (CML-CP) (NICOLI)
Primary Purpose
Chronic Myeloid Leukemia
Status
Completed
Phase
Phase 1
Locations
Germany
Study Type
Interventional
Intervention
Nilotinib, interferon-alfa
Sponsored by
About this trial
This is an interventional treatment trial for Chronic Myeloid Leukemia focused on measuring Chronic myeloid leukemia, interferon alfa, nilotinib, combination, CML, Philadelphia chromosome positive (Ph+) chronic myeloid leukemia patients in chronic phase (CML-CP) after switch from previous CML treatment
Eligibility Criteria
Inclusion Criteria:
- Patients with chronic myeloid leukemia in chronic phase (CML-CP) at screening
- Initial diagnosis of CML cytogenetically confirmed by the presence of the Ph+ metaphases from the bone marrow
- Patients who have been treated with nilotinib for a minimum of 6 months (1 month represents 28 days) after switch from previous CML treatments
- Patients who have been treated with stable dosing of 2x400mg nilotinib within the last month before start of study treatment
- No grade 3-4 CTC toxicities on nilotinib alone in the last month preceding the start of the study regimen
Exclusion Criteria:
- Patients who are considered Ph- because they do not have a confirmed cytogenetic diagnosis of the t(9;22) translocation in their bone marrow metaphases
- Evidence of a point mutation within the BCR-ABL gene leading to a clinically relevant amino acid exchange in the kinase domain at position T315 (gatekeeper mutation T315I)
- Impaired cardiac function
- Severe or uncontrolled medical conditions (i.e. uncontrolled diabetes, active or uncontrolled infection).
Other protocol-defined inclusion/exclusion criteria may apply
Sites / Locations
- Novartis Investigative Site
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
Nilotinib in conjunction with low dose interferon alfa
Arm Description
Outcomes
Primary Outcome Measures
Number of Clinically significant adverse events or abnormal laboratory values (dose-limiting toxicities) unrelated to disease progression, intercurrent illness, or concomitant medications on the combination treatment
Secondary Outcome Measures
Rate of major cytogenetic response (MCyR) at 6 and 12 months
Rate of complete cytogenetic response (CCyR) at 6 and 12 months
Rate of major molecular response (MMR) at 12 months
Safety profile of nilotinib in combination with interferon alfa, i.e. the number of dose limiting toxicities (DLT) for each interferon alfa dose level
Progression-free survival (PFS)
Event-free survival
Overall survival (OS)
Full Information
1. Study Identification
Unique Protocol Identification Number
NCT01220648
Brief Title
Determining the Maximum Tolerated Dose of Low Dose Interferon-alpha in Conjunction With Nilotinib in Pretreated Philadelphia Chromosome Positive (Ph+) Chronic Myeloid Leukemia Patients in Chronic Phase (CML-CP)
Acronym
NICOLI
Official Title
An Open Label, Nonrandomized, Single-center, Phase I Trial of Pretreated Philadelphia Chromosome Positive (Ph+) Chronic Myeloid Leukemia Patients in Chronic Phase (CML-CP) With Nilotinib in Combination With Low Dose Interferon-alpha (IFN) - NICOLI Study -
Study Type
Interventional
2. Study Status
Record Verification Date
May 2015
Overall Recruitment Status
Completed
Study Start Date
April 2012 (undefined)
Primary Completion Date
January 2014 (Actual)
Study Completion Date
January 2014 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Novartis Pharmaceuticals
4. Oversight
5. Study Description
Brief Summary
This study will assess the maximum tolerated dose of low dose interferon in conjunction with nilotinib in pretreated Philadelphia chromosome positive (Ph+) chronic myeloid leukemia patients in chronic phase (CML-CP).
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Chronic Myeloid Leukemia
Keywords
Chronic myeloid leukemia, interferon alfa, nilotinib, combination, CML, Philadelphia chromosome positive (Ph+) chronic myeloid leukemia patients in chronic phase (CML-CP) after switch from previous CML treatment
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 1
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
Non-Randomized
Enrollment
4 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Nilotinib in conjunction with low dose interferon alfa
Arm Type
Experimental
Intervention Type
Drug
Intervention Name(s)
Nilotinib, interferon-alfa
Other Intervention Name(s)
AMN107
Primary Outcome Measure Information:
Title
Number of Clinically significant adverse events or abnormal laboratory values (dose-limiting toxicities) unrelated to disease progression, intercurrent illness, or concomitant medications on the combination treatment
Time Frame
12 months
Secondary Outcome Measure Information:
Title
Rate of major cytogenetic response (MCyR) at 6 and 12 months
Time Frame
12 months
Title
Rate of complete cytogenetic response (CCyR) at 6 and 12 months
Time Frame
12 months
Title
Rate of major molecular response (MMR) at 12 months
Time Frame
12 months
Title
Safety profile of nilotinib in combination with interferon alfa, i.e. the number of dose limiting toxicities (DLT) for each interferon alfa dose level
Time Frame
12 months
Title
Progression-free survival (PFS)
Time Frame
12 months
Title
Event-free survival
Time Frame
12 months
Title
Overall survival (OS)
Time Frame
12 months
10. Eligibility
Sex
All
Minimum Age & Unit of Time
18 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Patients with chronic myeloid leukemia in chronic phase (CML-CP) at screening
Initial diagnosis of CML cytogenetically confirmed by the presence of the Ph+ metaphases from the bone marrow
Patients who have been treated with nilotinib for a minimum of 6 months (1 month represents 28 days) after switch from previous CML treatments
Patients who have been treated with stable dosing of 2x400mg nilotinib within the last month before start of study treatment
No grade 3-4 CTC toxicities on nilotinib alone in the last month preceding the start of the study regimen
Exclusion Criteria:
Patients who are considered Ph- because they do not have a confirmed cytogenetic diagnosis of the t(9;22) translocation in their bone marrow metaphases
Evidence of a point mutation within the BCR-ABL gene leading to a clinically relevant amino acid exchange in the kinase domain at position T315 (gatekeeper mutation T315I)
Impaired cardiac function
Severe or uncontrolled medical conditions (i.e. uncontrolled diabetes, active or uncontrolled infection).
Other protocol-defined inclusion/exclusion criteria may apply
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Novartis Pharmaceuticals
Organizational Affiliation
Novartis Pharmaceuticals
Official's Role
Study Director
Facility Information:
Facility Name
Novartis Investigative Site
City
Leipzig
ZIP/Postal Code
04103
Country
Germany
12. IPD Sharing Statement
Citations:
PubMed Identifier
19959083
Citation
Guilhot F, Roy L, Saulnier PJ, Guilhot J. Interferon in chronic myeloid leukaemia: past and future. Best Pract Res Clin Haematol. 2009 Sep;22(3):315-29. doi: 10.1016/j.beha.2009.10.005.
Results Reference
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Determining the Maximum Tolerated Dose of Low Dose Interferon-alpha in Conjunction With Nilotinib in Pretreated Philadelphia Chromosome Positive (Ph+) Chronic Myeloid Leukemia Patients in Chronic Phase (CML-CP)
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