Efficacy and Safety of DA-3002 in Children With Idiopathic Short Stature
Primary Purpose
Idiopathic Short Stature
Status
Completed
Phase
Phase 3
Locations
Study Type
Interventional
Intervention
DA-3002
Sponsored by
About this trial
This is an interventional treatment trial for Idiopathic Short Stature focused on measuring growth hormone
Eligibility Criteria
Inclusion Criteria:
- Chronological Age ≥ 4
- Bone Age <11 (for girls) and <13 (for boys)
- Height <3rd percentile for age
- normal thyroid function
Exclusion Criteria:
- endocrine and/or metabolic disorders
- growth failure caused by other disorders
- previous use of drugs that could interfere with Growth Hormone treatment
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm Type
Experimental
No Intervention
Arm Label
DA-3002 Treatment group
Non-treatment control group
Arm Description
1.11 IU(0.37mg)/kg bodyweight of DA-3002 per week given by subcutaneous injections (six or seven times per week)
Height be measured with no treatment
Outcomes
Primary Outcome Measures
Annualized Height Velocity(cm/Year) After 26 Weeks
Height Velocity calculated with height measured at Baseline and after 26 weeks was converted to annual growth rate.
Secondary Outcome Measures
Changes in Height Standard Deviation Score After 26 Weeks
The Height Standard Deviation Score was calculated as height minus reference mean height divided by the standard deviation of the reference mean height, both given by a reference growth table for the corresponding chronological age at the height measurement. Greater Height Standard Deviation Score indicates greater height.
Full Information
NCT ID
NCT01786902
First Posted
February 6, 2013
Last Updated
September 18, 2017
Sponsor
Dong-A ST Co., Ltd.
1. Study Identification
Unique Protocol Identification Number
NCT01786902
Brief Title
Efficacy and Safety of DA-3002 in Children With Idiopathic Short Stature
Official Title
Open, Multi-Center, Controlled, Randomized Phase III Clinical Trial to Evaluate the Efficacy and Safety of DA-3002(Recombinant Humn Growth Hormone)Treatment in Children With Idiopathic Short Stature
Study Type
Interventional
2. Study Status
Record Verification Date
September 2017
Overall Recruitment Status
Completed
Study Start Date
February 2012 (undefined)
Primary Completion Date
April 2014 (Actual)
Study Completion Date
April 2014 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Dong-A ST Co., Ltd.
4. Oversight
Data Monitoring Committee
No
5. Study Description
Brief Summary
Growth hormone therapy will improve the height of idiopathic short statured children. DA-3002(Recombinant Human Growth hormone)treated group for 26 weeks, will be compared to non-treatment group in efficacy and safety.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Idiopathic Short Stature
Keywords
growth hormone
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 3
Interventional Study Model
Parallel Assignment
Masking
None (Open Label)
Allocation
Randomized
Enrollment
70 (Actual)
8. Arms, Groups, and Interventions
Arm Title
DA-3002 Treatment group
Arm Type
Experimental
Arm Description
1.11 IU(0.37mg)/kg bodyweight of DA-3002 per week given by subcutaneous injections (six or seven times per week)
Arm Title
Non-treatment control group
Arm Type
No Intervention
Arm Description
Height be measured with no treatment
Intervention Type
Drug
Intervention Name(s)
DA-3002
Other Intervention Name(s)
Recombinant Human Growth Hormone
Primary Outcome Measure Information:
Title
Annualized Height Velocity(cm/Year) After 26 Weeks
Description
Height Velocity calculated with height measured at Baseline and after 26 weeks was converted to annual growth rate.
Time Frame
26 weeks
Secondary Outcome Measure Information:
Title
Changes in Height Standard Deviation Score After 26 Weeks
Description
The Height Standard Deviation Score was calculated as height minus reference mean height divided by the standard deviation of the reference mean height, both given by a reference growth table for the corresponding chronological age at the height measurement. Greater Height Standard Deviation Score indicates greater height.
Time Frame
26 weeks
Other Pre-specified Outcome Measures:
Title
Changes in Anti-growth Hormone Antibody
Time Frame
baseline and 26 weeks
10. Eligibility
Sex
All
Minimum Age & Unit of Time
4 Years
Maximum Age & Unit of Time
13 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Chronological Age ≥ 4
Bone Age <11 (for girls) and <13 (for boys)
Height <3rd percentile for age
normal thyroid function
Exclusion Criteria:
endocrine and/or metabolic disorders
growth failure caused by other disorders
previous use of drugs that could interfere with Growth Hormone treatment
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Hanwook Yoo, MD
Organizational Affiliation
Asan Medical Center
Official's Role
Principal Investigator
First Name & Middle Initial & Last Name & Degree
Byungkyu Suh, MD
Organizational Affiliation
Seoul St. Mary's Hospital
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Cheolwoo Ko, MD
Organizational Affiliation
Kyungpook National University Hospital
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Keehyoung Lee, MD
Organizational Affiliation
Korea University Anam Hospitial
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Dongkyu Jin, MD
Organizational Affiliation
Samsung Medical Center
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Choongho Shin, MD
Organizational Affiliation
Seoul National University Hospital
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Jinsoon Hwang, MD
Organizational Affiliation
Aju University Hospital
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Hoseong Kim, MD
Organizational Affiliation
Severance Children's Hospital Yonsei University
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Wooyoung Jeong, MD
Organizational Affiliation
Pusan University Hospital
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Chanjong Kim, MD
Organizational Affiliation
Chonnam National University Hospital
Official's Role
Study Director
First Name & Middle Initial & Last Name & Degree
Heonsuk Han, MD
Organizational Affiliation
Chungbuk National University Hospital
Official's Role
Study Director
12. IPD Sharing Statement
Learn more about this trial
Efficacy and Safety of DA-3002 in Children With Idiopathic Short Stature
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