Examination of the Lipid Metabolism of the Liver After Choline Substitution in Cystic Fibrosis
Primary Purpose
Cystic Fibrosis Liver Disease
Status
Completed
Phase
Not Applicable
Locations
Study Type
Interventional
Intervention
Choline Chloride
Sponsored by
About this trial
This is an interventional treatment trial for Cystic Fibrosis Liver Disease
Eligibility Criteria
Inclusion Criteria:
- Age > 18 years
- male
- Cystic fibrosis is verified
- pancreatic insufficiency
- Decline of plasma phosphatidylcholine and steatosis of the liver
- informed consent is given
Exclusion Criteria:
- cirrhosis of the liver
- Hyperreactivity to choline containing food
- allergic bronchopulmonary aspergillosis or other acute exacerbations of pulmonary infections
- FEV1 < 40%
- smoker
- chronic alcohol consume
- clinically relevant diseases (for example thyroid dysfunction, disturbance of lipid metabolism, renal diseases, significant left or right ventricular functional restriction) which will change the lipid metabolism of the liver
- Implants or other reasons which make magnetic resonance examinations impossible
Sites / Locations
Arms of the Study
Arm 1
Arm Type
Other
Arm Label
Choline Chloride
Arm Description
Patients receive choline chloride (1g Choline) three times a day for 12.6 weeks as a food supply
Outcomes
Primary Outcome Measures
Measurement of D9-Methyl-Choline Kinetic
The substitution of choline as a food supplement will augment the phosphatidylcholine and lipoprotein (VLDL) secretion of the liver into the blood and will therefore result in a reduction of the triglyceride retention in the liver
Secondary Outcome Measures
Lipid storage of the liver
Comparison of steatosis of the liver (measured by magnetic resonance spectroscopy or sonography) before to after the choline substitution
Augmentation of creatinine concentration within the calf muscle
Augmentation of creatine concentration within the calf muscle due to the choline substitution measured by magnetic resonance spectroscopy
FVC
Comparison of FVC before to after the choline substitution
FEV1
Comparison of FEV1 before to after the choline substitution
MEF25
Comparison of MEF25 before to after the choline substitution
MMEF
Comparison of MMEF before to after the choline substitution
Full Information
NCT ID
NCT03312140
First Posted
October 4, 2017
Last Updated
November 29, 2017
Sponsor
University Hospital Tuebingen
1. Study Identification
Unique Protocol Identification Number
NCT03312140
Brief Title
Examination of the Lipid Metabolism of the Liver After Choline Substitution in Cystic Fibrosis
Official Title
Examination of the Lipid Metabolism of the Liver After Choline Substitution in Cystic Fibrosis
Study Type
Interventional
2. Study Status
Record Verification Date
October 2017
Overall Recruitment Status
Completed
Study Start Date
November 6, 2014 (Actual)
Primary Completion Date
April 24, 2016 (Actual)
Study Completion Date
February 8, 2017 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
University Hospital Tuebingen
4. Oversight
Studies a U.S. FDA-regulated Drug Product
No
Studies a U.S. FDA-regulated Device Product
No
Data Monitoring Committee
No
5. Study Description
Brief Summary
Pilot study to investigate the effect of choline chloride in cystic fibrosis patients with liver steatosis by comparing their status before and after the intervention
Detailed Description
Within this single arm pilot study patients with cystic fibrosis and liver steatosis receive choline chloride (2x0.5 gram three times a day) as a food supply for 88 days. D9-choline metabolism is measured before and after the intervention phase. Hypothesis of the study is, that supplying choline augments the secretion of phosphatidyl choline and lipoprotein (VLDL) from the liver and therefore results in a measurable reduction of the triglyceride storage of the liver.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Cystic Fibrosis Liver Disease
7. Study Design
Primary Purpose
Treatment
Study Phase
Not Applicable
Interventional Study Model
Single Group Assignment
Model Description
Pilot study to evolve the effect ot the treatment by comparing data before and after the treatment within the same patients
Masking
None (Open Label)
Allocation
N/A
Enrollment
10 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Choline Chloride
Arm Type
Other
Arm Description
Patients receive choline chloride (1g Choline) three times a day for 12.6 weeks as a food supply
Intervention Type
Drug
Intervention Name(s)
Choline Chloride
Primary Outcome Measure Information:
Title
Measurement of D9-Methyl-Choline Kinetic
Description
The substitution of choline as a food supplement will augment the phosphatidylcholine and lipoprotein (VLDL) secretion of the liver into the blood and will therefore result in a reduction of the triglyceride retention in the liver
Time Frame
3 months
Secondary Outcome Measure Information:
Title
Lipid storage of the liver
Description
Comparison of steatosis of the liver (measured by magnetic resonance spectroscopy or sonography) before to after the choline substitution
Time Frame
3 months
Title
Augmentation of creatinine concentration within the calf muscle
Description
Augmentation of creatine concentration within the calf muscle due to the choline substitution measured by magnetic resonance spectroscopy
Time Frame
3 months
Title
FVC
Description
Comparison of FVC before to after the choline substitution
Time Frame
3 months
Title
FEV1
Description
Comparison of FEV1 before to after the choline substitution
Time Frame
3 months
Title
MEF25
Description
Comparison of MEF25 before to after the choline substitution
Time Frame
3 months
Title
MMEF
Description
Comparison of MMEF before to after the choline substitution
Time Frame
3 months
10. Eligibility
Sex
Male
Minimum Age & Unit of Time
18 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Age > 18 years
male
Cystic fibrosis is verified
pancreatic insufficiency
Decline of plasma phosphatidylcholine and steatosis of the liver
informed consent is given
Exclusion Criteria:
cirrhosis of the liver
Hyperreactivity to choline containing food
allergic bronchopulmonary aspergillosis or other acute exacerbations of pulmonary infections
FEV1 < 40%
smoker
chronic alcohol consume
clinically relevant diseases (for example thyroid dysfunction, disturbance of lipid metabolism, renal diseases, significant left or right ventricular functional restriction) which will change the lipid metabolism of the liver
Implants or other reasons which make magnetic resonance examinations impossible
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Joachim Riethmüller, PD
Organizational Affiliation
Klinik für Kinder- und Jugendmedizin Tübingen
Official's Role
Principal Investigator
12. IPD Sharing Statement
Learn more about this trial
Examination of the Lipid Metabolism of the Liver After Choline Substitution in Cystic Fibrosis
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