In Vivo Characterization of Macrophages in Pediatric Patients With Malignant Brain Tumors Using Ferumoxytol-enhanced MRI
Primary Purpose
Childhood Brain Neoplasm
Status
Withdrawn
Phase
Early Phase 1
Locations
Study Type
Interventional
Intervention
Diagnostic (ferumoxytol-enhanced MRI)
Surgery
Ferumoxytol
Tissue Analysis
Sponsored by
About this trial
This is an interventional diagnostic trial for Childhood Brain Neoplasm
Eligibility Criteria
Inclusion Criteria:
- Any patient with suspected malignant brain tumor on diagnostic MR imaging who will undergo a resection
Exclusion Criteria:
- Informed consent cannot be obtained either from the patient or legal representative
- Severe coexisting or terminal systemic disease that may interfere with the conduct of the study
- Contraindication to MRI (metal implants)
- Hemosiderosis/hemochromatosis
- Iron overload from any cause (not just hemosiderosis or hemochromatosis), even if secondary to frequent blood transfusions, severe chronic hemolysis, excess dietary or parenteral iron, or any other etiology
- Known hypersensitivity to ferumoxytol or any of its components
- Pregnant patients
Sites / Locations
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
Diagnostic (ferumoxytol-enhanced MRI)
Arm Description
All subjects in the experimental arm will have a single intravenous dose of ferumoxytol (5 mg Fe/kg), to be administered 24 hours before the subject undergoes ferumoxytol-enhanced magnetic resonance imaging (MRI). These subjects will subsequently undergo surgery, and tissue analysis of surgically resected samples (specifically the number of iron-containing and non-iron-containing macrophages) will be correlated with imaging features on ferumoxytol-enhanced MRI.
Outcomes
Primary Outcome Measures
Iron concentration measurements
Obtain susceptibility measurements and relaxation times (R2, R2*, R2') in patients receiving ferumoxytol.
Secondary Outcome Measures
Macrophages on histopathology
Determine the number of macrophages in tissue samples at histopathology.
Full Information
NCT ID
NCT03179449
First Posted
June 5, 2017
Last Updated
April 12, 2023
Sponsor
Michael Iv
Collaborators
National Cancer Institute (NCI)
1. Study Identification
Unique Protocol Identification Number
NCT03179449
Brief Title
In Vivo Characterization of Macrophages in Pediatric Patients With Malignant Brain Tumors Using Ferumoxytol-enhanced MRI
Official Title
MR Imaging of Inflammatory Responses in the Central Nervous System With Ferumoxytol-Enhanced MRI (Pediatric Brain Tumor Protocol)
Study Type
Interventional
2. Study Status
Record Verification Date
April 2023
Overall Recruitment Status
Withdrawn
Why Stopped
Accrual Factor
Study Start Date
July 1, 2017 (Actual)
Primary Completion Date
June 1, 2025 (Anticipated)
Study Completion Date
June 1, 2025 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor-Investigator
Name of the Sponsor
Michael Iv
Collaborators
National Cancer Institute (NCI)
4. Oversight
Studies a U.S. FDA-regulated Drug Product
Yes
Studies a U.S. FDA-regulated Device Product
No
Data Monitoring Committee
Yes
5. Study Description
Brief Summary
This pilot early phase I trial studies how well ferumoxytol-enhanced magnetic resonance imaging (MRI) correlates with inflammatory (macrophage) responses in pediatric patients with malignant brain tumors. If there is good correlation, ferumoxytol-enhanced MRI can serve as a noninvasive imaging biomarker of inflammation.
Detailed Description
PRIMARY OBJECTIVE:
I. To establish the magnetic resonance (MR) imaging signal characteristics of macrophages in pediatric patients (>= 2 years old) with newly diagnosed malignant brain tumors using ferumoxytol, an ultrasmall superparamagnetic iron oxide (USPIO) particle.
SECONDARY OBJECTIVES:
I. To correlate the MRI signal of ferumoxytol uptake in macrophages with the number of macrophages in surgical tumor specimen at histopathology.
OUTLINE:
Patients receive a single intravenous infusion of ferumoxytol over 15 minutes. After 24 hours, patients undergo ferumoxytol-enhanced magnetic resonance imaging (MRI). Patients will then undergo MRI-localized tissue sampling and tumor resection.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Childhood Brain Neoplasm
7. Study Design
Primary Purpose
Diagnostic
Study Phase
Early Phase 1
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
0 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Diagnostic (ferumoxytol-enhanced MRI)
Arm Type
Experimental
Arm Description
All subjects in the experimental arm will have a single intravenous dose of ferumoxytol (5 mg Fe/kg), to be administered 24 hours before the subject undergoes ferumoxytol-enhanced magnetic resonance imaging (MRI). These subjects will subsequently undergo surgery, and tissue analysis of surgically resected samples (specifically the number of iron-containing and non-iron-containing macrophages) will be correlated with imaging features on ferumoxytol-enhanced MRI.
Intervention Type
Diagnostic Test
Intervention Name(s)
Diagnostic (ferumoxytol-enhanced MRI)
Other Intervention Name(s)
CONTRAST ENHANCED MRI, Contrast-enhanced MRI
Intervention Description
Undergo ferumoxytol-enhanced MRI
Intervention Type
Procedure
Intervention Name(s)
Surgery
Intervention Description
Undergo surgical resection
Intervention Type
Drug
Intervention Name(s)
Ferumoxytol
Other Intervention Name(s)
Feraheme, FERUMOXYTOL NON-STOICHIOMETRIC MAGNETITE
Intervention Description
Given IV
Intervention Type
Other
Intervention Name(s)
Tissue Analysis
Intervention Description
Correlative analysis for macrophage detection and quantification. This applies for all patients in the experimental arm who undergo ferumoxytol infusion.
Primary Outcome Measure Information:
Title
Iron concentration measurements
Description
Obtain susceptibility measurements and relaxation times (R2, R2*, R2') in patients receiving ferumoxytol.
Time Frame
Day 1
Secondary Outcome Measure Information:
Title
Macrophages on histopathology
Description
Determine the number of macrophages in tissue samples at histopathology.
Time Frame
Days 2-4
10. Eligibility
Sex
All
Minimum Age & Unit of Time
2 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Any patient with suspected malignant brain tumor on diagnostic MR imaging who will undergo a resection
Exclusion Criteria:
Informed consent cannot be obtained either from the patient or legal representative
Severe coexisting or terminal systemic disease that may interfere with the conduct of the study
Contraindication to MRI (metal implants)
Hemosiderosis/hemochromatosis
Iron overload from any cause (not just hemosiderosis or hemochromatosis), even if secondary to frequent blood transfusions, severe chronic hemolysis, excess dietary or parenteral iron, or any other etiology
Known hypersensitivity to ferumoxytol or any of its components
Pregnant patients
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Michael Iv
Organizational Affiliation
Stanford University
Official's Role
Principal Investigator
12. IPD Sharing Statement
Plan to Share IPD
No
Learn more about this trial
In Vivo Characterization of Macrophages in Pediatric Patients With Malignant Brain Tumors Using Ferumoxytol-enhanced MRI
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