Palifermin for Patients Receiving Hematopoietic Stem Cell Transplantation
Primary Purpose
Mucositis
Status
Unknown status
Phase
Phase 3
Locations
Study Type
Interventional
Intervention
Palifermin
Sponsored by
About this trial
This is an interventional prevention trial for Mucositis focused on measuring Hematopoietic stem cell transplantation, Palifermin
Eligibility Criteria
Inclusion Criteria:
- adequate organ function
- patients who will receive autologous stem cell transplantation
- patients who will receive allogeneic stem cell transplantation using myeloablative conditioning regimen
Exclusion Criteria:
- presence of concomitant malignancy
- presence of active infection or oral mucositis prior to stem cell transplantation
- any conditions where the severity of oral mucositis cannot be evaluated
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm Type
Active Comparator
Placebo Comparator
Arm Label
Palifermin
Normal saline
Arm Description
The patients belong to this arm will be given palifermin, keratinocyte growth factor, in addition to the conventional supportive care for oral mucositis. Palifermin will be given at a dose of 60 mcg/kg for 3 days before commencement of the preparative regimen and for 3 days after stem cell infusion
The patients belong to this arm will be given normal saline as placebo plus conventional supportive care for oral mucositis. Normal saline will be given at the same volume and schedule with the study drug.
Outcomes
Primary Outcome Measures
Duration of severe oral mucositis after stem cell transplantation
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Secondary Outcome Measures
Incidence of severe oral mucositis after stem cell transplantation
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Average VAS score during severe oral mucositis
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Requirement of opioid drugs during severe oral mucositis
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Requirement of opioid drugs
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Cost effectiveness of palifermin during stem cell transplantation
from admission for stem cell transplantation to discharge
Quality of life during transplant period
1 week before stem cell infusion to discharge
Full Information
NCT ID
NCT02313792
First Posted
December 5, 2014
Last Updated
December 8, 2014
Sponsor
The Catholic University of Korea
Collaborators
BLNH
1. Study Identification
Unique Protocol Identification Number
NCT02313792
Brief Title
Palifermin for Patients Receiving Hematopoietic Stem Cell Transplantation
Official Title
Efficacy, Safety and Quality of Life of Palifermin on Reducing Oral Mucositis in Patients With Hematopoietic Stem Cell Transplantation, Prospective Double-blind Randomized Phase III Trial
Study Type
Interventional
2. Study Status
Record Verification Date
December 2014
Overall Recruitment Status
Unknown status
Study Start Date
January 2015 (undefined)
Primary Completion Date
March 2015 (Anticipated)
Study Completion Date
June 2015 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Principal Investigator
Name of the Sponsor
The Catholic University of Korea
Collaborators
BLNH
4. Oversight
Data Monitoring Committee
No
5. Study Description
Brief Summary
The purpose of this study is to compare the efficacy and safety of palifermin on reducing mucositis for patients receiving autologous or allogeneic stem cell transplantation with supportive care.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Mucositis
Keywords
Hematopoietic stem cell transplantation, Palifermin
7. Study Design
Primary Purpose
Prevention
Study Phase
Phase 3
Interventional Study Model
Single Group Assignment
Masking
ParticipantCare ProviderInvestigatorOutcomes Assessor
Allocation
Randomized
Enrollment
88 (Anticipated)
8. Arms, Groups, and Interventions
Arm Title
Palifermin
Arm Type
Active Comparator
Arm Description
The patients belong to this arm will be given palifermin, keratinocyte growth factor, in addition to the conventional supportive care for oral mucositis. Palifermin will be given at a dose of 60 mcg/kg for 3 days before commencement of the preparative regimen and for 3 days after stem cell infusion
Arm Title
Normal saline
Arm Type
Placebo Comparator
Arm Description
The patients belong to this arm will be given normal saline as placebo plus conventional supportive care for oral mucositis. Normal saline will be given at the same volume and schedule with the study drug.
Intervention Type
Drug
Intervention Name(s)
Palifermin
Primary Outcome Measure Information:
Title
Duration of severe oral mucositis after stem cell transplantation
Description
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Time Frame
5 weeks
Secondary Outcome Measure Information:
Title
Incidence of severe oral mucositis after stem cell transplantation
Description
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Time Frame
5 weeks
Title
Average VAS score during severe oral mucositis
Description
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Time Frame
5 weeks
Title
Requirement of opioid drugs during severe oral mucositis
Description
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Time Frame
5 weeks
Title
Requirement of opioid drugs
Description
from onset of severe oral mucositis till resolution of the mucositis or 28 days after stem cell transplantation
Time Frame
5 weeks
Title
Cost effectiveness of palifermin during stem cell transplantation
Description
from admission for stem cell transplantation to discharge
Time Frame
5 weeks
Title
Quality of life during transplant period
Description
1 week before stem cell infusion to discharge
Time Frame
5 weeks
10. Eligibility
Sex
All
Minimum Age & Unit of Time
16 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
adequate organ function
patients who will receive autologous stem cell transplantation
patients who will receive allogeneic stem cell transplantation using myeloablative conditioning regimen
Exclusion Criteria:
presence of concomitant malignancy
presence of active infection or oral mucositis prior to stem cell transplantation
any conditions where the severity of oral mucositis cannot be evaluated
12. IPD Sharing Statement
Learn more about this trial
Palifermin for Patients Receiving Hematopoietic Stem Cell Transplantation
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