Safety and Efficacy of Fremanezumab for Migraine in Adult CADASIL
Primary Purpose
Cadasil, Migraine
Status
Withdrawn
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
Fremanezumab
Placebo
Sponsored by
About this trial
This is an interventional treatment trial for Cadasil
Eligibility Criteria
Inclusion Criteria
- Age 18 to 70 years old
- English speaking
- Diagnosis of CADASIL confirmed by presence of a pathogenic NOTCH3 gene mutation
- Diagnosis of migraine for at least 12 months and diagnosis of chronic migraine for at least 28 days according to the International Classification of Headache Disorders
- MIDAS score of >10 points
- Ability to provide written informed consent
Exclusion Criteria
- History of ischemic stroke within 4 weeks of screening assessment
- Screening blood pressure >150 mm Hg
- Use of onabotulinum toxin A 4 months prior to trial or other injectable/stimulatory/magnetic method of headache control
- Use of opiates or barbiturates 4 days prior to trial
- Patients with competing intracerebral pathology (e.g. history of intracerebral hemorrhage, multiple sclerosis)
- NYHA Class III or IV congestive heart failure
- History of myocardial infarction
- History of coronary bypass surgery or coronary stenting
- Pregnancy or breastfeeding
- Contraindication to undergoing brain MRI per standard clinical practice guidelines
- Vulnerable populations, including incarcerated inmates, dementia, and inability to provide consent
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm Type
Active Comparator
Placebo Comparator
Arm Label
Subjects with CADASIL treatment intervention
Subjects with CADASIL placebo intervention
Arm Description
Subjects that have been diagnosed with both CADASIL and moderately to severely disabling migraine headaches will be treated with Fremanezumab injections.
Subjects that have been diagnosed with both CADASIL and moderately to severely disabling migraine headaches will be treated with placebo injections.
Outcomes
Primary Outcome Measures
Change in migraine-related disability
Measured using the The Migraine Disability Assessment (MIDAS) questionnaire which is a brief, self-administered questionnaire designed to quantify headache-related disability over a 3 month period using number of days
Change in headache intensity
Measured using Headache Impact Test (HIT)-6 scores with the answers being never, rarely, sometimes, very often or always and equating to 6, 8, 10, 11, and 13 points respectively. Each answer is summated to equal the final score.
Adverse events
Number of adverse events reported
Secondary Outcome Measures
Full Information
1. Study Identification
Unique Protocol Identification Number
NCT04334408
Brief Title
Safety and Efficacy of Fremanezumab for Migraine in Adult CADASIL
Official Title
A Phase II Double-Blinded Placebo Controlled Individual Subject Stepped Wedge Clinical Trial Evaluating the Safety and Efficacy of Fremanezumab for Migraine in Adult CADASIL
Study Type
Interventional
2. Study Status
Record Verification Date
February 2022
Overall Recruitment Status
Withdrawn
Why Stopped
Lack of funding to support the trial.
Study Start Date
December 2021 (Anticipated)
Primary Completion Date
December 2024 (Anticipated)
Study Completion Date
December 2024 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Principal Investigator
Name of the Sponsor
Mayo Clinic
4. Oversight
Studies a U.S. FDA-regulated Drug Product
Yes
Studies a U.S. FDA-regulated Device Product
No
Data Monitoring Committee
No
5. Study Description
Brief Summary
Researchers are trying to find out more about the side effects of fremanezumab when treating patients with Cerebral Autosomal Dominant Arteriopathy with Subcortical Infarcts and Leukoencephalopathy (CADASIL) for migraine headaches.
Detailed Description
Subjects will receive 4 to 20 weeks of placebo injections followed by 12 weeks of monthly administered fremanezumab by subcutaneous injection (225 mg split four weeks apart for 12 weeks). Following completion of the 12 weeks of therapy, the participant will return to placebo for the washout period. Both the patient and the investigator will be blinded to the timing of transition to and from placebo and the transition to and from fremanezumab.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Cadasil, Migraine
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Crossover Assignment
Masking
ParticipantInvestigator
Allocation
Randomized
Enrollment
0 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Subjects with CADASIL treatment intervention
Arm Type
Active Comparator
Arm Description
Subjects that have been diagnosed with both CADASIL and moderately to severely disabling migraine headaches will be treated with Fremanezumab injections.
Arm Title
Subjects with CADASIL placebo intervention
Arm Type
Placebo Comparator
Arm Description
Subjects that have been diagnosed with both CADASIL and moderately to severely disabling migraine headaches will be treated with placebo injections.
Intervention Type
Drug
Intervention Name(s)
Fremanezumab
Other Intervention Name(s)
Ajovy
Intervention Description
Subjects will receive a single dose total 225 mg (1 injection of 225 mg per 1.5 mL injection) followed by a single dose of 225 mg (1 1.5mL injection) at four week intervals. Both the subject and the investigator will be blinded to the timing of transition to and from placebo and the transition to and from fremanezumab.
Intervention Type
Drug
Intervention Name(s)
Placebo
Intervention Description
Placebo injections during the run in and washout serves as the control condition. Both the subject and the investigator will be blinded to the timing of transition to and from placebo and the transition to and from fremanezumab.
Primary Outcome Measure Information:
Title
Change in migraine-related disability
Description
Measured using the The Migraine Disability Assessment (MIDAS) questionnaire which is a brief, self-administered questionnaire designed to quantify headache-related disability over a 3 month period using number of days
Time Frame
Baseline, 2 week intervals up to 48 weeks
Title
Change in headache intensity
Description
Measured using Headache Impact Test (HIT)-6 scores with the answers being never, rarely, sometimes, very often or always and equating to 6, 8, 10, 11, and 13 points respectively. Each answer is summated to equal the final score.
Time Frame
Baseline, 2 week intervals up to 48 weeks
Title
Adverse events
Description
Number of adverse events reported
Time Frame
48 weeks
10. Eligibility
Sex
All
Minimum Age & Unit of Time
18 Years
Maximum Age & Unit of Time
70 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria
Age 18 to 70 years old
English speaking
Diagnosis of CADASIL confirmed by presence of a pathogenic NOTCH3 gene mutation
Diagnosis of migraine for at least 12 months and diagnosis of chronic migraine for at least 28 days according to the International Classification of Headache Disorders
MIDAS score of >10 points
Ability to provide written informed consent
Exclusion Criteria
History of ischemic stroke within 4 weeks of screening assessment
Screening blood pressure >150 mm Hg
Use of onabotulinum toxin A 4 months prior to trial or other injectable/stimulatory/magnetic method of headache control
Use of opiates or barbiturates 4 days prior to trial
Patients with competing intracerebral pathology (e.g. history of intracerebral hemorrhage, multiple sclerosis)
NYHA Class III or IV congestive heart failure
History of myocardial infarction
History of coronary bypass surgery or coronary stenting
Pregnancy or breastfeeding
Contraindication to undergoing brain MRI per standard clinical practice guidelines
Vulnerable populations, including incarcerated inmates, dementia, and inability to provide consent
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
James F Meschia
Organizational Affiliation
Mayo Clinic
Official's Role
Principal Investigator
12. IPD Sharing Statement
Plan to Share IPD
No
Links:
URL
https://www.mayo.edu/research/clinical-trials
Description
Mayo Clinic Clinical Trials
Learn more about this trial
Safety and Efficacy of Fremanezumab for Migraine in Adult CADASIL
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