Study of Efficacy and Safety of Canakinumab in Pediatric Patients With Kawasaki Disease
Primary Purpose
Kawasaki Disease
Status
Withdrawn
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
Canakinumab
Sponsored by
About this trial
This is an interventional treatment trial for Kawasaki Disease focused on measuring Kawasaki disease, Coronary artery aneurysm, mucocutaneous lymph node syndrome, lymph node syndrome, canakinumab, intravenous immunoglobulin naïve (IVIG-naïve), intravenous immunoglobulin refractory (IVIG-refractory), pediatric
Eligibility Criteria
Key Inclusion Criteria:
-Active Kawasaki disease defined as:
- fever ≥38.5°C for ≥5 days
- four out of five of the following criteria: (i) conjunctival injection, (ii) oral mucous membrane changes, (e.g., injected pharynx, or strawberry tongue), (iii) erythema of hands or feet, (iv) polymorphous rash, (v) cervical lymphadenopathy
Key Exclusion Criteria:
Patients fulfilling any of the following criteria are not eligible for inclusion in this study:
- Previous Kawasaki Disease diagnosis, refractory and/or incomplete Kawasaki disease (for IVIG-naïve patients, Cohort 1)
- Patients who had fever for longer than a week (for Intravenous Immunoglobulin-naïve patients, Cohort 1), or longer than 14 days (for Intravenous Immunoglobulin-refractory patients, Cohort 2)
- History of hypersensitivity to any of the study drugs or to drugs or similar chemical classes or excipients (e.g. citric acid and anhydrous sodium chloride disodium edetate dehydrate polysorbate 80; sodium hydroxide; water for injections)
Other protocol-defined inclusion/exclusion may apply.
Sites / Locations
Arms of the Study
Arm 1
Arm Type
Experimental
Arm Label
Kawasaki patients
Arm Description
Outcomes
Primary Outcome Measures
resolution of fever
Secondary Outcome Measures
proportion of patients with C-reactive Protein reduction
proportion of patients developing coronary artery aneurysms
time to resolution of fever
proportion of patients with remittent fever
size of coronary artery aneurysm
Coronary artery aneurysm evolution over time
proportion of patients with coronary artery aneurysm
Full Information
NCT ID
NCT02980263
First Posted
October 24, 2016
Last Updated
February 15, 2017
Sponsor
Novartis Pharmaceuticals
1. Study Identification
Unique Protocol Identification Number
NCT02980263
Brief Title
Study of Efficacy and Safety of Canakinumab in Pediatric Patients With Kawasaki Disease
Official Title
Study of Efficacy and Safety of Canakinumab in Pediatric Patients With Kawasaki Disease
Study Type
Interventional
2. Study Status
Record Verification Date
February 2017
Overall Recruitment Status
Withdrawn
Study Start Date
November 15, 2016 (Anticipated)
Primary Completion Date
November 30, 2017 (Anticipated)
Study Completion Date
November 30, 2017 (Anticipated)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Novartis Pharmaceuticals
4. Oversight
Data Monitoring Committee
Yes
5. Study Description
Brief Summary
The purpose of this trial is to evaluate whether, in Intravenous Immunoglobulin-naïve or refractory patients diagnosed with active Kawasaki disease, administration of canakinumab controls fever and acute phase reactants.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Kawasaki Disease
Keywords
Kawasaki disease, Coronary artery aneurysm, mucocutaneous lymph node syndrome, lymph node syndrome, canakinumab, intravenous immunoglobulin naïve (IVIG-naïve), intravenous immunoglobulin refractory (IVIG-refractory), pediatric
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Single Group Assignment
Masking
None (Open Label)
Allocation
N/A
Enrollment
0 (Actual)
8. Arms, Groups, and Interventions
Arm Title
Kawasaki patients
Arm Type
Experimental
Intervention Type
Drug
Intervention Name(s)
Canakinumab
Other Intervention Name(s)
ACZ885
Primary Outcome Measure Information:
Title
resolution of fever
Time Frame
Day 3/4
Secondary Outcome Measure Information:
Title
proportion of patients with C-reactive Protein reduction
Time Frame
12 weeks
Title
proportion of patients developing coronary artery aneurysms
Time Frame
12 weeks
Title
time to resolution of fever
Time Frame
12 weeks
Title
proportion of patients with remittent fever
Time Frame
12 weeks
Title
size of coronary artery aneurysm
Time Frame
24 weeks
Title
Coronary artery aneurysm evolution over time
Time Frame
12 weeks
Title
proportion of patients with coronary artery aneurysm
Time Frame
12 weeks
10. Eligibility
Sex
All
Minimum Age & Unit of Time
28 Days
Maximum Age & Unit of Time
10 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Key Inclusion Criteria:
-Active Kawasaki disease defined as:
fever ≥38.5°C for ≥5 days
four out of five of the following criteria: (i) conjunctival injection, (ii) oral mucous membrane changes, (e.g., injected pharynx, or strawberry tongue), (iii) erythema of hands or feet, (iv) polymorphous rash, (v) cervical lymphadenopathy
Key Exclusion Criteria:
Patients fulfilling any of the following criteria are not eligible for inclusion in this study:
Previous Kawasaki Disease diagnosis, refractory and/or incomplete Kawasaki disease (for IVIG-naïve patients, Cohort 1)
Patients who had fever for longer than a week (for Intravenous Immunoglobulin-naïve patients, Cohort 1), or longer than 14 days (for Intravenous Immunoglobulin-refractory patients, Cohort 2)
History of hypersensitivity to any of the study drugs or to drugs or similar chemical classes or excipients (e.g. citric acid and anhydrous sodium chloride disodium edetate dehydrate polysorbate 80; sodium hydroxide; water for injections)
Other protocol-defined inclusion/exclusion may apply.
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Novartis Pharmaceuticals
Organizational Affiliation
Novartis Pharmaceuticals
Official's Role
Study Director
12. IPD Sharing Statement
Plan to Share IPD
Undecided
Learn more about this trial
Study of Efficacy and Safety of Canakinumab in Pediatric Patients With Kawasaki Disease
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