A Confirmatory Safety and Efficacy Study of BBI-4000 in Subjects With Axillary Hyperhidrosis
Primary Purpose
Hyperhidrosis
Status
Completed
Phase
Phase 2
Locations
Study Type
Interventional
Intervention
BBI-4000 gel, 5%
BBI-4000 gel, 10%
BBI-4000 gel, 15%
Vehicle (Placebo)
Sponsored by
About this trial
This is an interventional treatment trial for Hyperhidrosis focused on measuring sweat gland disease, sweating, underarm
Eligibility Criteria
Inclusion Criteria:
- Male or female subject ≥ 18 years of age.
- Diagnosis of primary axillary hyperhidrosis that meets the following criteria: (a) symptoms of hyperhydrosis for at least 6 months' duration, (b) HDSM-Ax of 3 - 4, (c) HDSS of 3 or 4 and (d) a minimum GSP of 50 mg is each axilla with a combined total of at least 150 mg.
- The ability to understand and follow all study-related procedures including study drug administration.
- Sexually active female of childbearing potential (FOCBP)* must agree to periodic pregnancy testing and use a medically acceptable method of contraception while receiving protocol-assigned product.
Exclusion Criteria:
- In the Investigators opinion, any skin or subcutaneous tissue conditions of the axilla(s).
- Prior use of any prohibited medication(s) or procedure(s) within the specified timeframe for the treatment of axillary hyperhidrosis.
- Anticholinergic agents used to treat conditions such as, but not limited to, hyperhidrosis, asthma, incontinence, gastrointestinal cramps, and muscular spasms by any route of administration.
- Use of potent inhibitors of cytochrome P450 CYP3A and CYP2D6.
- Use of any cholinergic drug (e.g. bethanechol) within 30 days.
- Known cause of hyperhidrosis or known history of a condition that may cause hyperhidrosis (i.e., hyperhidrosis secondary to any known cause such hyperthyroidism, diabetes mellitus, medications, etc.).
- Subjects with unstable diabetes mellitus or thyroid disease, history of renal or hepatic impairment, malignancy glaucoma, intestinal obstructive or motility disease, obstructive uropathy, myasthenia gravis, BPH, neurological or psychiatric conditions, Sjögren's or Sicca syndrome, or cardiac abnormalities that may alter or exacerbate sweat production by the use of anticholinergics in the investigator's opinion.
- Subjects with known hypersensitivity to glycopyrrolate, anticholinergics, or any of the components of the topical formulation.
- Subject is pregnant, lactating or is planning to become pregnant during the study.
- History or presence of supraventricular tachycardia, ventricular arrhythmias, atrial fibrillation or atrial flutter.
Sites / Locations
Arms of the Study
Arm 1
Arm 2
Arm 3
Arm 4
Arm Type
Experimental
Experimental
Experimental
Placebo Comparator
Arm Label
BBI-4000 gel, 5%
BBI-4000 gel, 10%
BBI-4000 gel, 15%
Vehicle
Arm Description
BBI-4000 gel, 5% applied once to each axilla daily
BBI-4000 gel, 10% applied once to each axilla daily
BBI-4000 gel, 15% applied once to each axilla daily
Placebo, applied once to each axilla daily
Outcomes
Primary Outcome Measures
Change of Hyperhidrosis Disease Severity Measure-Axillary (HDSM-Ax) Score From Baseline to End of Therapy
11 question evaluation tool to assess the effect of BBI-4000 gel, 5%, 10% and 15 % on hyperhidrosis disease severity measures in subjects with axillary hyperhidrosis. Two questions measured the frequency (since yesterday) of underarm sweating outcomes. The range of responses included increasing frequency scale: None of the time (0); A little of the time (1); Some of the time (2); Most of the time (3); All of the time (4). The next seven questions measured the severity of underarm sweating outcomes. Range in increasing severity: I did not experience this (0); Mild (1); Moderate (2); Severe (3); Very Severe (4). The last two questions measured the need to change or clean from underarm sweating. Range in increasing degree of need: Not at all (0); Slight (1); Moderate (2); Strong (3); Very Strong (4).
The mean was derived by taking the total score and dividing by the number of questions answered. A negative LSM reflects a reduction, decrease or measured improvement in HDSM-Ax
Number (%) of Subjects Reporting at Least One Treatment Emergent Adverse Event by Severity
Subjects reporting more than one adverse event are counted only once using the highest severity.
Secondary Outcome Measures
Average Gravimetrically Measured Sweat Production (GSP) Observed by Visit, Per Protocol Population
Measured weight of the amount of sweat produced by Visit Method of calculating average for Baseline, End of Therapy, and End of Therapy Imputed.
Baseline GSP was defined as the mean of any available Visit 2, Visit 3, and Visit 4 values (occurring Days -21 to -7 relative to Day 1 Baseline) End of Therapy is defined as the mean of any available Day 41, Day 42, and Day 43 values.
Full Information
NCT ID
NCT03024255
First Posted
January 6, 2017
Last Updated
April 20, 2023
Sponsor
Botanix Pharmaceuticals
1. Study Identification
Unique Protocol Identification Number
NCT03024255
Brief Title
A Confirmatory Safety and Efficacy Study of BBI-4000 in Subjects With Axillary Hyperhidrosis
Official Title
A Multicenter, Randomized, Double-Blinded, Vehicle-Controlled Study to Evaluate the Safety and Efficacy of 3 Concentrations of Topically Applied BBI-4000 (Sofpironium Bromide) Gel in Subjects With Axillary Hyperhidrosis
Study Type
Interventional
2. Study Status
Record Verification Date
April 2023
Overall Recruitment Status
Completed
Study Start Date
December 22, 2016 (Actual)
Primary Completion Date
September 19, 2017 (Actual)
Study Completion Date
September 19, 2017 (Actual)
3. Sponsor/Collaborators
Responsible Party, by Official Title
Sponsor
Name of the Sponsor
Botanix Pharmaceuticals
4. Oversight
Data Monitoring Committee
No
5. Study Description
Brief Summary
This study is being conducted to assess the safety and efficacy of 3 concentrations of BBI-4000 and vehicle (4 treatment arms), applied for the treatment of axillary hyperhidrosis.
Detailed Description
This is a Multicenter, Randomized, Double Blind, Vehicle-Controlled Study to Evaluate the Safety and Efficacy of 3 concentrations of Topically Applied BBI-4000 in Subjects with Axillary Hyperhidrosis.
Safety will be assessed through collection of vital signs, adverse events, local skin responses, hematology, serum chemistry laboratory testing and urinalysis.
6. Conditions and Keywords
Primary Disease or Condition Being Studied in the Trial, or the Focus of the Study
Hyperhidrosis
Keywords
sweat gland disease, sweating, underarm
7. Study Design
Primary Purpose
Treatment
Study Phase
Phase 2
Interventional Study Model
Parallel Assignment
Masking
ParticipantCare ProviderInvestigatorOutcomes Assessor
Allocation
Randomized
Enrollment
227 (Actual)
8. Arms, Groups, and Interventions
Arm Title
BBI-4000 gel, 5%
Arm Type
Experimental
Arm Description
BBI-4000 gel, 5% applied once to each axilla daily
Arm Title
BBI-4000 gel, 10%
Arm Type
Experimental
Arm Description
BBI-4000 gel, 10% applied once to each axilla daily
Arm Title
BBI-4000 gel, 15%
Arm Type
Experimental
Arm Description
BBI-4000 gel, 15% applied once to each axilla daily
Arm Title
Vehicle
Arm Type
Placebo Comparator
Arm Description
Placebo, applied once to each axilla daily
Intervention Type
Drug
Intervention Name(s)
BBI-4000 gel, 5%
Other Intervention Name(s)
BBI-4000 Low Concentration
Intervention Description
BBI-4000 gel, 5% applied once to each axilla daily
Intervention Type
Drug
Intervention Name(s)
BBI-4000 gel, 10%
Other Intervention Name(s)
BBI-4000 Medium Concentration
Intervention Description
BBI-4000 gel, 10% applied once to each axilla daily
Intervention Type
Drug
Intervention Name(s)
BBI-4000 gel, 15%
Other Intervention Name(s)
BBI-4000 High Concentration
Intervention Description
BBI-4000 gel, 15% applied once to each axilla daily
Intervention Type
Drug
Intervention Name(s)
Vehicle (Placebo)
Other Intervention Name(s)
Control
Intervention Description
Placebo, applied once to each axilla daily
Primary Outcome Measure Information:
Title
Change of Hyperhidrosis Disease Severity Measure-Axillary (HDSM-Ax) Score From Baseline to End of Therapy
Description
11 question evaluation tool to assess the effect of BBI-4000 gel, 5%, 10% and 15 % on hyperhidrosis disease severity measures in subjects with axillary hyperhidrosis. Two questions measured the frequency (since yesterday) of underarm sweating outcomes. The range of responses included increasing frequency scale: None of the time (0); A little of the time (1); Some of the time (2); Most of the time (3); All of the time (4). The next seven questions measured the severity of underarm sweating outcomes. Range in increasing severity: I did not experience this (0); Mild (1); Moderate (2); Severe (3); Very Severe (4). The last two questions measured the need to change or clean from underarm sweating. Range in increasing degree of need: Not at all (0); Slight (1); Moderate (2); Strong (3); Very Strong (4).
The mean was derived by taking the total score and dividing by the number of questions answered. A negative LSM reflects a reduction, decrease or measured improvement in HDSM-Ax
Time Frame
overall ~6 Weeks, as listed in description includes: Baseline-Visit 1, Visit 4 and End of Therapy Visit - Days 41, 42, 43.
Title
Number (%) of Subjects Reporting at Least One Treatment Emergent Adverse Event by Severity
Description
Subjects reporting more than one adverse event are counted only once using the highest severity.
Time Frame
Treatment initiation through end of treatment (~42 days) and subsequent safety f/u (~14 days following end of treatment)
Secondary Outcome Measure Information:
Title
Average Gravimetrically Measured Sweat Production (GSP) Observed by Visit, Per Protocol Population
Description
Measured weight of the amount of sweat produced by Visit Method of calculating average for Baseline, End of Therapy, and End of Therapy Imputed.
Baseline GSP was defined as the mean of any available Visit 2, Visit 3, and Visit 4 values (occurring Days -21 to -7 relative to Day 1 Baseline) End of Therapy is defined as the mean of any available Day 41, Day 42, and Day 43 values.
Time Frame
Visit 2, 3, and 4 timepoints were reported Days -21 to -7, relative to Visit 5/ Day 1/Baseline, Days 8, 15, 22, 29, 36, 41, 42, 43, and 57
10. Eligibility
Sex
All
Minimum Age & Unit of Time
18 Years
Accepts Healthy Volunteers
No
Eligibility Criteria
Inclusion Criteria:
Male or female subject ≥ 18 years of age.
Diagnosis of primary axillary hyperhidrosis that meets the following criteria: (a) symptoms of hyperhydrosis for at least 6 months' duration, (b) HDSM-Ax of 3 - 4, (c) HDSS of 3 or 4 and (d) a minimum GSP of 50 mg is each axilla with a combined total of at least 150 mg.
The ability to understand and follow all study-related procedures including study drug administration.
Sexually active female of childbearing potential (FOCBP)* must agree to periodic pregnancy testing and use a medically acceptable method of contraception while receiving protocol-assigned product.
Exclusion Criteria:
In the Investigators opinion, any skin or subcutaneous tissue conditions of the axilla(s).
Prior use of any prohibited medication(s) or procedure(s) within the specified timeframe for the treatment of axillary hyperhidrosis.
Anticholinergic agents used to treat conditions such as, but not limited to, hyperhidrosis, asthma, incontinence, gastrointestinal cramps, and muscular spasms by any route of administration.
Use of potent inhibitors of cytochrome P450 CYP3A and CYP2D6.
Use of any cholinergic drug (e.g. bethanechol) within 30 days.
Known cause of hyperhidrosis or known history of a condition that may cause hyperhidrosis (i.e., hyperhidrosis secondary to any known cause such hyperthyroidism, diabetes mellitus, medications, etc.).
Subjects with unstable diabetes mellitus or thyroid disease, history of renal or hepatic impairment, malignancy glaucoma, intestinal obstructive or motility disease, obstructive uropathy, myasthenia gravis, BPH, neurological or psychiatric conditions, Sjögren's or Sicca syndrome, or cardiac abnormalities that may alter or exacerbate sweat production by the use of anticholinergics in the investigator's opinion.
Subjects with known hypersensitivity to glycopyrrolate, anticholinergics, or any of the components of the topical formulation.
Subject is pregnant, lactating or is planning to become pregnant during the study.
History or presence of supraventricular tachycardia, ventricular arrhythmias, atrial fibrillation or atrial flutter.
Overall Study Officials:
First Name & Middle Initial & Last Name & Degree
Patricia Walker, MD PhD
Organizational Affiliation
Botanix Pharmaceuticals
Official's Role
Study Director
12. IPD Sharing Statement
Plan to Share IPD
No
Learn more about this trial
A Confirmatory Safety and Efficacy Study of BBI-4000 in Subjects With Axillary Hyperhidrosis
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