Study of BHV-3241 in Participants With Multiple System Atrophy (M-STAR)
Multiple System Atrophy
About this trial
This is an interventional treatment trial for Multiple System Atrophy focused on measuring Multiple System Atrophy (MSA)
Eligibility Criteria
Inclusion Criteria:
- Diagnosis of probable or possible MSA according to consensus clinical criteria (Gilman et al 2008), including subjects with MSA of either subtype (MSA-P or MSA-C).
- Able to ambulate without the assistance of another person, defined as the ability to take at least 10 steps. Use of assistive devices (e.g., walker or cane) is allowed.
- Anticipated survival of at least 3 years at the time of Screening, as judged by the Investigator.
Exclusion Criteria:
- Any condition that would interfere with the subject's ability to comply with study instructions, place the subject at unacceptable risk, and/or confound the interpretation of safety or efficacy data from the study, as judged by the Investigator.
- Diagnosis of neurological disorders, other than MSA.
Sites / Locations
- Barrow Neurological Institute
- UC San Diego Department of Neurosciences
- UCLA Medical Center / Neurological Services
- Stanford University
- UCSF Memory and Aging Center
- Rocky Mountain Movement Disorders Center
- Parkinson's Disease and Movement Disorders Center of Boca Raton
- University of Florida
- Mayo Clinic Florida
- University of South Florida
- Emory University
- Rush University Medical Center
- University of Chicago
- University of Kansas Medical Center
- John Hopkins University
- Massachusetts General Hospital
- Beth Israel Deaconess Medical Center
- Lahey Hospital & Medical Center
- QUEST Research Institute
- Mayo Clinic
- Albany Medical College
- NYU School of Medicine, NYU Dysautonomia Center
- Columbia University Medical Center, Neurological Institute
- Pennsylvania State University Hershey Medical Center
- Parkinson's Disease and Movement Disorders Center at the University of Pennsylvania
- Vanderbilt University Medical Center
- Kerwin Research Center
- UT Southwestern Medical Center
- Swedish Medical Center
- Confraternitaet Privatklinik Josefstadt in Wien
- University Clinic Innsbruck
- CHU de Bordeaux, Service de Neurologie
- CHU - Hospital de la Timone
- Unité d'investigation clinique de Neurologie Rez-de-jardin, Bloc Hopital CHU Pontchaillou
- Hopitaux Universitaire de Strasbourg-Centre de References des Maladies Autoimmunes
- CHU Purpan
- University Hospital of Liepzig
- St. Josef - Hospital Bochum, Kardiologische Studienambulanz
- Deutsches Zentrum für Neurodegenerative Erkrankungen (DZNE)
- University Hospital Duesseldorf
- CRC Core Facility Medizinische Hochschule Hannover (MHH)
- Paracelsus-Elena-Klinik
- Klinik für Neurologie - UKSH - Campus Kiel
- Universitaetsklinikum Giessen und Marburg GmbH - Parkinson-Studienzentrum, Klinik für Neurologie
- Universitaetsklinikum Muenster
- Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico di Milano
- A.O.U. San Giovanni di Dio e Ruggi d'Aragona
- The Newcastle upon Tyne Hospitals NHS Foundation Trust - Campus for Ageing and Vitality (NGH)
Arms of the Study
Arm 1
Arm 2
Experimental
Placebo Comparator
Verdiperstat
Placebo
Participants received verdiperstat 300 mg tablet orally once daily for 1 week, followed by 300 mg twice daily for 1 week, and then 600 mg twice daily for the remaining 46 weeks of the double-blind phase. Participants who completed the double-blind phase were offered the opportunity to enroll in an open-label extension (OLE) phase to continue verdiperstat 600 mg twice daily for 48 weeks.
Participants received placebo matching with verdiperstat for 48 weeks. Participants who completed the double-blind phase were offered the opportunity to enroll in an OLE phase to receive verdiperstat 600 mg tablet orally twice daily for 48 weeks.